Received: 8 August 2017 Revised: 14 November 2017 Accepted: 26 December 2017
DOI: 10.1111/ahg.12244
SHORT COMMUNICATION
A novel homozygous missense variant in NECTIN4 (PVRL4)
causing ectodermal dysplasia cutaneous syndactyly syndrome
Farooq Ahmad
1,2
Abdul Nasir
1
Holger Thiele
3
Muhammad Umair
1
Guntram Borck
2
Wasim Ahmad
1
1
Department of Biochemistry, Faculty of Bio-
logical Sciences, Quaid-i-Azam University,
Islamabad, Pakistan
2
Institute of Human Genetics, University of
Ulm, Ulm, Germany
3
Cologne Center for Genomics (CCG), Uni-
versity of Cologne, Cologne, Germany
Correspondence
Wasim Ahmad, PhD, Department of Biochem-
istry, Faculty of Biological Sciences, Quaid-i-
Azam University, Islamabad, Pakistan.
Email: wahmad@qau.edu.pk
Guntram Borck, MD, PhD, Institute of Human
Genetics, University of Ulm, Albert-Einstein-
Allee 11, 89081 Ulm, Germany.
Email: guntram.borck@uni-ulm.de
Funding information
This work was supported by a grant from the
Higher Education Commission (HEC), Islam-
abad, Pakistan. FA was supported by the HEC-
sponsored International Research Support
Initiative Program (IRSIP).
Abstract
Ectodermal dysplasia syndactyly syndrome 1 (EDSS1) is a rare form of ectodermal
dysplasia including anomalies of hair, nails, and teeth along with bilateral cutaneous
syndactyly of hands and feet. In the present report, we performed a clinical and genetic
characterization of a consanguineous Pakistani family with four individuals affected
by EDSS1. We performed exome sequencing using DNA of one affected individual.
Exome data analysis identified a novel homozygous missense variant (c.242T>C;
p.(Leu81Pro)) in NECTIN4 (PVRL4). Sanger sequencing validated this variant and
confirmed its cosegregation with the disease phenotype in the family members. Thus,
our report adds a novel variant to the NECTIN4 mutation spectrum and contributes to
the NECTIN4-related clinical characterization.
KEYWORDS
consanguinity, ectodermal dysplasia syndactyly syndrome 1, EDSS1, homozygous, mutation, NECTIN4
1 INTRODUCTION
Ectodermal dysplasias (EDs) present a large clinically and
genetically heterogeneous group of congenital developmen-
tal dystrophies of ectodermal derived appendages including
hair, nails, teeth, and sweat glands. More than 200 clini-
cally distinct conditions of EDs and ED syndromes have been
described, with an estimated cumulative incidence rate of 7 in
10,000 births (Itin & Fistarol, 2004).
Isolated and syndromic forms of EDs are characterized
by particular clinical hallmarks. Mutations in cell–cell adhe-
sion molecule-encoding genes have been reported as the
cause of ED syndromes such as human juvenile macular
dystrophy (HJMD; OMIM#601553) caused by mutations
in the CDH3 gene (Ahmad et al., 2016), characterized by
hypotrichosis followed by progressive degeneration of the
central retina leading to blindness; and cleft lip/palate ED
(CLPED1; OMIM#225060) and ED syndactyly syndrome
(EDSS1; OMIM#613573) due to mutations in NECTIN1 (pre-
viously known as PVRL1) and NECTIN4 (previously known
as PVRL4), respectively (Brancati et al., 2010; Suzuki et al.,
2000). EDSS1 is characterized by bilateral partial cutaneous
syndactyly of the hands and feet, sparse to absent scalp hair
and eyebrows and eyelashes, abnormal dentition (i.e., peg-
shaped and conical crowns and early tooth loss), hypoplas-
tic nails and palmoplantar keratoderma; whereas facial and
dental anomalies, hypotrichosis, palmoplantar hyperkeratosis,
dysplastic nails, syndactyly, and cleft lip/cleft palate are seen
in CLPED1. Only 7 NECTIN4 mutations have thus far been
described in EDSS1; thus, no clear-cut genotype-phenotype
correlations have yet been described.
In the present study, we describe a large consanguineous
family of Pakistani origin displaying clinical features of
EDSS1. We identified a novel homozygous NECTIN4 mis-
sense variant (c.242T>C, p.(Leu81Pro)) segregating with the
disease.
Ann Hum Genet. 2018;1–7. © 2018 John Wiley & Sons Ltd/University College London 1 wileyonlinelibrary.com/journal/ahg