Vol.:(0123456789) 1 3
Rheumatology International
https://doi.org/10.1007/s00296-020-04596-3
OBSERVATIONAL RESEARCH
Patient satisfaction and clinical efectiveness of switching
from intravenous tocilizumab to subcutaneous tocilizumab in patients
with juvenile idiopathic arthritis: an observational study
Nuray Aktay Ayaz
1
· Şerife Gül Karadağ
2
· Rahime Koç
2
· Fatma Gül Demirkan
2
· Figen Çakmak
1
·
Hafze Emine Sönmez
2
Received: 1 April 2020 / Accepted: 4 May 2020
© Springer-Verlag GmbH Germany, part of Springer Nature 2020
Abstract
Introduction Juvenile idiopathic arthritis (JIA) is a heterogeneous group of idiopathic infammatory arthritis afecting chil-
dren younger than 16 years of age. Tocilizumab (TCZ) is a humanized anti-interleukin 6 (IL-6) receptor antibody that was
approved for systemic and polyarticular JIA patients. However, the studies regarding patients’ satisfaction while receiving
TCZ therapy is scarce. Herein, we aimed to evaluate the efect of subcutaneous (SC) TCZ administration on patient satisfac-
tion and disease control of JIA patients.
Methods All JIA patients receiving TCZ were included in the study. Clinical features, laboratory fndings and JADAS71
scores were recorded at baseline and every 3 months during follow-up. Nine of the patients on intravenous (IV) TCZ treat-
ment were switched to SC form. All patients receiving TCZ-SC were questioned by a clinical nurse specialist (CNS) to
assess patient satisfaction.
Results A total of 39 patients receiving TCZ were included in the study. Among them, treatment of nine patients (fve female,
four male) was switched to SC form with a median of 11.5 (8–69) months after initiation of TCZ. Patients were stable both
clinically and in laboratory means at the 3rd month of TCZ-SC treatment. There was no deterioration in terms of active joint
counts, physician’s VAS, patient’s VAS and JADAS71. According to patient satisfaction questionnaire, eight of the patients
felt satisfed with SC administrations in terms of life quality, school success and reduced school absenteeism. However, one
patient did not agree that the SC form is as efective as IV form and wanted to continue with IV form.
Conclusion TCZ is an efective treatment option in JIA and switching from IV to SC route when necessary is found to be
an efective and acceptable alternative by the patients as well.
Keywords Tocilizumab · Patient satisfaction · Subcutaneous
Introduction
Juvenile idiopathic arthritis is a heterogeneous group of
disease characterized by arthritis of unknown origin with
onset before age of 16 years. The major target of JIA treat-
ment is hindering long-term disabilities by overcoming
the ongoing infammation. Conventional treatment of JIA
includes non-steroidal anti-infammatory drugs (NSAIDs),
corticosteroids, and disease modifying anti-rheumatic drugs
(DMARDs) such as methotrexate, sulfasalazine and lefuno-
mide [1, 2]. Even though, DMARDs are still the frst line
treatments [2, 3], some patients could not achieve remission
with DMARDs and in the presence of inadequate response,
biologic agents (BA) emerge as an alternative [1, 2].
Rheumatology
INTERNATIONAL
Electronic supplementary material The online version of this
article (https://doi.org/10.1007/s00296-020-04596-3) contains
supplementary material, which is available to authorized users.
* Nuray Aktay Ayaz
nurayaktay@gmail.com
1
Department of Pediatric Rheumatology, Istanbul University
Medical School, Fatih, Istanbul, Turkey
2
Department of Pediatric Rheumatology, Kanuni Sultan
Süleyman Research and Training Hospital, University
of Health Sciences, Istanbul, Turkey