Changes in outcomes (1996 –2004) for pediatric oncology and hematopoietic stem cell transplant patients requiring invasive mechanical ventilation Robert F. Tamburro, MD; Raymond C. Barfield, MD; Michele L. Shaffer, PhD; Surender Rajasekaran, MD; Paul Woodard, MD; R. Ray Morrison, MD; Scott C. Howard, MD; Richard T. Fiser, MD; Jeffrey C. Schmidt, MD; Elaine M. Sillos, MD A lthough cancer is responsible for more deaths in children 1 yr of age than any other dis- ease, outcomes are improving (1, 2). Over the past 4 decades in the United States, outcomes for children di- agnosed with cancer have progressed from an estimated 80% mortality to an 80% survival (2). Moreover, hematopoi- etic stem cell transplantation (HSCT) is being employed for an ever-expanding list of malignant and nonmalignant diseases (3). These advancements have resulted in an increased need for critical care ser- vices for these children. In fact, nearly 40% of pediatric cancer patients require intensive care services, accounting for approximately 3% of all pediatric inten- sive care unit (PICU) admissions (4, 5). Additionally, 10% to 25% of allogeneic pediatric HSCT patients require mechan- ical ventilation (6 –11). Historically, these children have been considered poor candidates for intensive care interventions, most notably those re- quiring mechanical ventilation due to re- spiratory failure. Data from the 1980s sug- gested that mortality rates for pediatric oncology patients requiring mechanical ventilation approached 75% (12, 13), with mortality rates approximating 90% for HSCT patients (14 –19). Over time, how- ever, outcomes have improved, particularly Objective: To assess the following hypotheses regarding me- chanically ventilated pediatric oncology patients, including those receiving hematopoietic stem cell transplant (HSCT) and those not receiving HSCT: 1) outcomes are more favorable for nontransplant oncology patients than for those requiring HSCT; 2) outcomes have improved for both populations over time; and 3) there are factors available during the time of mechanical ventilation that identify patients with a higher likelihood of dying. Design: Retrospective review. Setting: Free-standing, tertiary care, pediatric hematology on- cology hospital. Patients: All patients requiring invasive mechanical ventilation with a diagnosis of cancer or following HSCT from January 1996 to December 2004. Interventions: Bivariate and multivariate analysis. Dates of admission were grouped into time periods for analysis: 1996 – 1998, 1999 –2001, and 2002–2004. Measurements and Main Results: There were 401 courses of mechanical ventilation (329 patients) analyzed. Forty-five percent of HSCT admissions (92 of 206) vs. 75% of non-HSCT oncology admissions (146 of 195) were extubated and discharged from the pediatric intensive care unit (p < .0001). Twenty-five percent of HSCT vs. 60% of non-HSCT admissions survived 6 months ( p < .0001). Among admissions with an abnormal chest radiograph and a PaO 2 /FIO 2 ratio <200, pediatric intensive care unit survival in- creased for each successive time period, with 45% of HSCT and 83% of non-HSCT admissions surviving during 2002–2004. In multivariate analysis of all study patients, Pediatric Risk of Mor- tality scores on the day of intubation, allogeneic HSCT, cardio- vascular failure, hepatic failure, neurologic failure, a previous course of mechanical ventilation within 6 months, and the time period intubated were associated with mortality. With the excep- tion of time period, these same variables were associated with mortality in multivariate analysis of only HSCT patients. Conclusions: HSCT patients who require mechanical ventila- tion have worse outcomes than non-HSCT oncology patients. Outcomes for both groups have improved over time. Allogeneic transplant, higher Pediatric Risk of Mortality scores, need for repeated mechanical ventilation, and concomitant organ system dysfunction are risk factors for death. (Pediatr Crit Care Med 2008; 9:●●●●●●) KEY WORDS: hematopoietic stem cell transplantation; cancer; critically ill; mechanical ventilation; respiratory failure; pediatrics; mortality From Penn State Children’s Hospital, Pediatrics, Division of Critical Care Medicine (RFT); St. Jude Children’s Research Hospital, Division of Bone Mar- row Transplantation (RCB, PW), Division of Critical Care Medicine (SR, RRM), and Department of He- matology Oncology (SCH); Penn State College of Medicine, Departments of Health Evaluation Sci- ences and Pediatrics (MLS); University of Arkansas for Medical Sciences, Pediatrics, Division of Critical Care Medicine (RTF); Pediatrix Medical Group of Colorado (JCS); and Baylor College of Medicine, Department of Pediatrics (EMS). Supported, in part, by the National Institutes of Health Cancer Center Support Core Grant CA 21765 and by the American Lebanese Syrian Associated Charities (ALSAC). The authors have not disclosed any potential con- flicts of interest. For information regarding this article, E-mail: rtamburro@psu.edu Copyright © 2008 by the Society of Critical Care Medicine and the World Federation of Pediatric Inten- sive and Critical Care Societies DOI: 10.1097/PCC.0b013e31816c7260 1 Pediatr Crit Care Med 2008 Vol. 9, No. 3 Abst balt5/zk8-pcc/zk8-pcc/zk800308/zk83085-07z xppws S1 4/5/08 5:51 Art: 200073 <ARTICLE DOCTOPICClinical InvestigationsDOCSUBJ DATEMay 2008VID9ISS3PPF PPL DOI10.1097/PCC.0b013e31816c7260>