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COMMUNICATION
M13 Bacteriophage and Adeno-Associated Virus Hybrid
for Novel Tissue Engineering Material with Gene
Delivery Functions
So Young Yoo,* Hyo-Eon Jin, Dong Shin Choi, Masae Kobayashi, Yohan Farouz,
Sky Wang, and Seung-Wuk Lee*
Dr. S. Y. Yoo, Dr. H.-E. Jin, D. S. Choi, M. Kobayashi,
Y. Farouz, S. Wang, Prof. S.-W. Lee
Department of Bioengineering
University of California, Berkeley
Physical Biosciences Division
Lawrence Berkeley National Laboratory
Berkeley Nanoscience and Nanoengineering Institute
Berkeley, CA 94720, USA
E-mail: yoosy@pusan.ac.kr; leesw@berkeley.edu
Dr. S. Y. Yoo
BIO-IT Foundry Technology Institute
Pusan National University
Busan 609-735, and Research Institute
for Convergence of Biomedical Science and Technology
Yangsan 626-770, Republic of Korea
Y. Farouz
Biology Department
Ecole Polytechnique Route de Saclay
91128, Palaiseau, Cedex, France
DOI: 10.1002/adhm.201500179
infect even by these virus-based approaches.
[10]
(2) Viruses often
cause host immune responses that eliminate the infecting virus
and its side effects on the surrounding cells. Gene delivery vec-
tors must be able to escape the body's natural surveillance sys-
tems, otherwise a resulting adverse immune reaction can cause
serious illness or even death.
[11]
(3) Random insertion of viral
genome into host genome can cause unexpected mutations
that can give rise to abnormal cell formation such as cancer.
[12]
Therefore, selective, safe, stable, and predictable gene delivery is
still challenging in terms of developing targeted gene delivery.
Recent advances in the phage biotechnology provide remark-
able pathways to develop novel biomaterials. Phages possess
many desirable features that make them attractive as versatile
gene delivery materials. Phage have little harmful effects and
are easily removed from the body through lysosomal degrada-
tion processes, causing few known side-effects.
[13]
Phage can be
modified to display functional peptide motifs on their minor
(pIII, pIX) and major (pVIII) coat proteins.
[14–18]
Large quanti-
ties of identical phage building blocks can be easily prepared
through bacterial amplification. Due to their long-filamentous
shape (aspect ratio: 130), phage can self-assemble into nanofi-
brous tissue-like matrix structures. Recently, we engineered
various biochemical cues (i.e., RGD (Arg-Gly-Asp), IKVAV (Ile-
Lys-Val-Ala-Val), and DGEA (Asp-Gly-Glu-Ala)) on major coat
proteins (pVIII) of the phage and developed self-assembled
tissue engineering materials for regulating cellular behaviors
of desired cells.
[15,16,19–22]
Using this phage-based tissue matrix
system, we demonstrated that engineered phages could regulate
various cellular behaviors such as proliferation and differentia-
tion.
[14–16,19,20,23]
Here, we developed novel tissue engineering
materials with gene delivery functions through the hybridiza-
tion of M13 bacteriophage (phage) and AAV. We engineered the
M13 phage with RGD peptide on the major coat proteins. We
then fused its gene with AAV gene with eukaryotic invading
functional gene, ITR. The resulting M13–AAV hybrid phage
exhibited enhanced internalization into target cells as compared
to minor coat engineered phage with RGD or wild-type phage.
The resulting hybrid phage formed nanofibrous matrices that
could support the cellular growth and deliver desired gene
information into the target tissues. Our novel M13–AAV hybrid
phage matrices can provide selective, stable, and safe gene
delivery ( Figure 1). We believe that it can be also developed as a
topical therapeutic tissue patch in the future.
In order to construct a novel phage tissue engineering mate-
rial with gene delivery function ( Figure 2), we constructed the
hybrid phage (M13
RGD8
–AAV
GFP
) carrying both RGD major coat
Reprogramming of cellular functions through gene delivery
is critical in treating cellular/tissue abnormalities as well as in
studying the mechanism of cellular behavior of many cells.
[1]
Many researchers have utilized nanosized natural
[2]
or syn-
thetic materials such as surfactants,
[3]
peptide or protein nano-
spheres,
[4]
and polymersomes for gene delivery.
[5]
Recently,
virus-based gene delivery vehicles, such as retrovirus or adeno-
virus, are considered as promising delivery vehicles for transfer
of genetic information into target cells.
[6]
Among them, adeno-
associated virus (AAV) has been largely adapted for therapeutic
gene transfer due to its innocuousness and high resistance to
extreme conditions.
[7]
The AAV is a nonpathogenic virus with
a linear single-stranded DNA genome that contains eukaryotic
gene integrating functional genes, named inverted terminal
repeats (ITRs; 145 bp in length for AAV2),
[8]
at each end of the
AAV viral genome terminus. The ITR possesses a T-shaped
hairpin structure with self-complementary guanine-cyto-
sine rich sequences; the gene enables integration of the viral
genome into as well as rescue from a specific section of the host
genome (19th chromosome in humans).
[9]
Despite the develop-
ment of various viral gene delivery vehicles, their therapeutic
application still remains challenging due to several reasons. (1)
Viruses can hardly reach their desired targets. Viruses have lim-
ited ranges of the type of host cells they can infect, although
adenoviruses and AAV are able to infect a relatively broad range
of cells efficiently. Still, some cell types are unmanageable to
Adv. Healthcare Mater. 2015,
DOI: 10.1002/adhm.201500179
www.advhealthmat.de
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