TE671 Cell-based ELISA for Anti-Acetylcholine Receptor Antibody Determination in Myasthenia Gravis Diego Franciotta, 1* Gianvito Martino, 2 Elena Brambilla, 3 Elisabetta Zardini, 1 Vera Locatelli, 1 Alessandra Bergami, 2 Carmine Tinelli, 4 Gaetano Desina, 5 and Vittorio Cosi 6 Background: Acetylcholine receptor (AChR) from hu- man muscles is the antigen used currently in radioim- munoprecipitation assays (RIPAs) for the determination of anti-AChR antibodies in the diagnosis of myasthenia gravis (MG). Our aim was to develop and validate an ELISA using TE671 cells as the source of AChR. Methods: After TE671 cell homogenization, the crude AChR extract was used for plate coating. Anti-AChR antibodies were determined in 207 MG patients and in 77 controls. Results: The mean intra- and interassay CVs (for two samples with different anti-AChR antibody concentra- tions) were 9.7% and 15.7%, respectively. Test sensitivity and specificity, for generalized MG, were 79.5% (95% confidence interval, 72.8 – 85.0%) and 96.1% (89.0 –99.1%). The detection limit was 2 nmol/L. Anti-AChR antibody concentrations from 53 MG patients, as tested with our ELISA, showed good agreement with an RIPA with a mean difference (SD) of 1.0 (5.6) nmol/L. Conclusion: Our ELISA is a simple screening test for the diagnosis of MG and enables rapid and inexpensive patient follow-up. © 1999 American Association for Clinical Chemistry Circulating antibodies to the acetylcholine receptor (AChR) 7 are essentially polyclonal and heterogeneous IgG, and rec- ognize diverse epitopes of the skeletal muscle nicotinic AChR. These antibodies are pathogenic in myasthenia gra- vis (MG) (1), a disease characterized by fatigability and relative weakness of voluntary muscles. Up to 90% of patients with generalized MG, and a lower percentage of those with ocular MG, have detectable serum concentrations of anti-AChR antibodies. The quantification of these anti- bodies is currently used as a laboratory support for diagno- sis, therapy monitoring, and follow-up in MG. Antibody concentration is commonly determined by exploitation of the ability of anti-AChR antibodies to immunoprecipitate- solubilized human muscle AChR, which, in turn, is com- plexed with 125 I-labeled -bungarotoxin ( 125 I--BuTx), a po- tent acetylcholine antagonist. The main disadvantages of this sensitive method are the use of radioisotopes and the limited availability of human muscles. Furthermore, the presence of -BuTx deprives a part of the anti-AChR anti- bodies of potential binding sites. Various authors have proposed alternative solid-phase immunoenzymatic methods to overcome some of the above- mentioned limitations. One method involves the coating of polystyrene wells directly with muscle extracts (2); another method uses muscle-derived AChR, which in turn is cap- tured by means of precoating with -BuTx (3) or with anti-AChR monoclonal antibodies (4). The main drawbacks of these methods are the paucity of AChR in relation to other muscle proteins (2) and the inadequacy of AChR capture, whether by -BuTx or by anti-AChR monoclonal antibodies (3, 4). The effect of these drawbacks is a reduction in the diagnostic sensitivity of these methods. 1 Laboratory of Neuroimmunology and 6 Division B, Istituto di Ricovero e Cura a Carattere Scientifico, Neurological Institute ‘Mondino’, via Palestro 3, University of Pavia, 27100 Pavia, Italy. 2 Experimental Neuroimmunotherapy and 3 Neuroimmunology Unit, De- partment of Biotechnology, San Raffaele Scientific Institute, via Olgettina 58, 20132 Milan, Italy. 4 Unit of Biometric, Istituto di Ricovero e Cura a Carattere Scientifico, Policlinico S. Matteo, University of Pavia, 27100 Pavia, Italy. 5 ‘Casa Sollievo della Sofferenza’, 71013 San Giovanni Rotondo (FG), Italy. *Author for correspondence. Fax 39-0382-380286; e-mail francid@ cpbim1.unipv.it. Received June 1, 1998; accepted December 28, 1998. 7 Nonstandard abbreviations: AChR, acetylcholine receptor; MG, myasthe- nia gravis; 125 I--BuTx, 125 I-labeled -bungarotoxin; RIPA, radioimmunopre- cipitation assay; SLE, systemic lupus erythematosus; and PBS, phosphate- buffered saline. Clinical Chemistry 45:3 400 – 405 (1999) Clinical Immunology 400