178 Current Drug Targets, 2009, 10, 178-192
1389-4501/09 $55.00+.00 © 2009 Bentham Science Publishers Ltd.
Current Treatment and Drug Discovery Against Leishmania spp. and
Plasmodium spp.: A Review
Angela Kaysel Cruz
1,
*
, Juliano Simões de Toledo
1
, Mofolusho Falade
2
, Mônica Cristina Terrão
1
,
Sumalee Kamchonwongpaisan
2
, Dennis E. Kyle
3
and Chairat Uthaipibull
2
1
Department of Cell and Molecular Biology and Pathogens, School of Medicine, University of São Paulo at Ribeirão
Preto, Av Bandeirantes, 3900, 14049900, São Paulo, Brazil;
2
Protein-Ligand Engineering and Molecular Biology Labo-
ratory, National Center for Genetic Engineering and Biotechnology, 113 Thailand Science Park, Phaholyothin Road,
Klong 1, Klong Luang, Pathumthani 12120 Thailand and
3
Department of Global Health, College of Public Health, Uni-
versity of South Florida, 3720 Spectrum Blvd, Suite 304, Tampa, FL 33612, USA
Abstract: Malaria and leishmaniasis are the most prevalent tropical diseases caused by protozoan parasites. Half of
world’s population is at risk of malaria and more than 2 million of new cases of leishmaniasis occur annually. There are
no vaccines available for these diseases and current treatments suffer from several limitations. Therefore, novel drugs for
malaria and leishmaniasis are much-needed. This article reviews the agents currently in use for treatment of these dis-
eases, their known mechanisms of action and weaknesses. We present an overview of the main strategies for drug discov-
ery and the relevance of these parasites genomics/proteomics data for a rational search of molecular targets and matching
leads. In this direction, we emphasize the importance of the highly integrated partnerships and networks between scientists
in academic institutions and industry involving several countries that promise to increase the chances of success and en-
hance cost-effectiveness in drug discovery against these parasitic diseases. In addition, we approach the available assays
for testing lead compounds in large scale and their limitations for they represent one of the bottlenecks in the pipeline for
novel drug discovery. We conclude the article presenting a recent coordinated initiative (TDR Transfection Network) es-
tablished to overcome some of these limitations by the generation of Plasmodium and Leishmania transgenic parasites
better suited for HTS platforms.
Key Words: Leishmaniasis, malaria, chemotherapy, drug discovery, molecular targets.
1. LEISHMANIASIS AND MALARIA EPIDEMIOL-
OGY
The World Health Organization (WHO) estimates that
one sixth of the world's population is suffering from ne-
glected tropical diseases [1]. The precarious life conditions,
the social disorganization and the lack of an effective politi-
cal action and educational programs contribute to persistence
of these diseases in the poorest regions of the world. Malaria
and leishmaniasis are the most prevalent neglected diseases
caused by protozoan parasites. Half of world’s population is
at risk of malaria. More than 500 million of people become
severely ill with nearly a million people die due to plasmo-
dium infection every year. Currently, leishmaniasis threatens
350 million of people around the world; more than 2 million
of new cases of leishmaniasis occur annually (http://www.
who.int/tdr/diseases/leish/diseaseinfo.htm). Brazil, India,
Bangladesh and Sudan present 90% of cases of visceral
leishmaniasis around the world. According to WHO, in the
last two decades the number of cases of leishmaniasis in-
creased due to the widening of endemic areas and the emer-
*Address correspondence to this author at the Departamento de Biologia
Celular e Molecular e Bioagentes Patogênicos, Faculdade de Medicina de
Ribeirão Preto, Universidade de São Paulo, Av. Bandeirantes, no. 3900,
CEP 14049-900 Ribeirão Preto, SP, Brazil; Tel: +55 16 3602 3318; Fax:
+55 l6 3633 1786; E-mail: akcruz@fmrp.usp.br
gence of new focus of leishmaniasis. Epidemiological stud-
ies indicate that deforesting, unsettled growth of urban cen-
ters and changing habits of the insect vector are contributing
to disease urbanization and new endemic foci [2-4].
Seventeen Leishmania species known to infect humans
are distributed in 88 countries around the world. In Brazil,
among the 14 species of Leishmania identified 10 are known
to infect human beings. Depending on several factors, which
includes the species of Leishmania and the host immune
response, the pathology caused by Leishmania can vary from
asymptomatic and mild cutaneous self-healing forms, diffuse
cutaneous leishmaniasis, or the mucosal form of the disease,
to the severe visceral (or Kala-azar) leishmaniasis, which is
fatal if not treated [5-8].
Malaria remains a public health problem of enormous
magnitude in tropical and subtropical regions of the world:
WHO estimates the number of new cases annually to be
about 247 million from about 3.3 billion people at risk. Of
these, nearly a million deaths occur, mostly in children under
the age of 5 and pregnant women. The population exposed to
the risk of this pernicious infection extends from Africa,
where the greatest burden exists, Southeast Asia, Papua New
Guinea and South America. The burden of infection is high-
est in sub-Saharan Africa owing to poverty and poor health-
care. In these highly affected areas, the majority of hospital