© 2006 Nature Publishing Group
Palindromic assembly of the giant muscle protein
titin in the sarcomeric Z-disk
Peijian Zou
1
*, Nikos Pinotsis
1,2
*, Stephan Lange
3,4
, Young-Hwa Song
1
, Alexander Popov
1
, Irene Mavridis
2
,
Olga M. Mayans
1,5
, Mathias Gautel
3
& Matthias Wilmanns
1
The Z-disk of striated and cardiac muscle sarcomeres is one of
the most densely packed cellular structures in eukaryotic cells
1
.
It provides the architectural framework for assembling and
anchoring the largest known muscle filament systems by an
extensive network of protein–protein interactions, requiring an
extraordinary level of mechanical stability. Here we show, using
X-ray crystallography, how the amino terminus of the longest
filament component, the giant muscle protein titin, is assembled
into an antiparallel (2:1) sandwich complex by the Z-disk ligand
telethonin. The pseudosymmetric structure of telethonin medi-
ates a unique palindromic arrangement of two titin filaments, a
type of molecular assembly previously found only in protein–
DNAcomplexes. We have confirmed its unique architecture in vivo
by protein complementation assays, and in vitro by experiments
using fluorescence resonance energy transfer. The model proposed
may provide a molecular paradigm of how major sarcomeric
filaments are crosslinked, anchored and aligned within complex
cytoskeletal networks.
The Z-disk of the sarcomere defines the lateral boundary of
sarcomeric units within the myocyte cytoskeleton. In higher verte-
brates it anchors and aligns at least three major sarcomeric filament
systems, including actin, titin and nebulin
1,2
. It also harbours many
smaller protein components, some of which, including a-actinin and
telethonin, have been mapped to distinct binding sites at the N
terminus of titin
3–7
. Their presence, proper sorting and localization
within the Z-disk region are critical for myofibril assembly and for
the maintenance of an intact Z-disk structure
8
. Components of
the Z-disk are also involved in signalling processes that may regulate
muscle development and degradation, as well as in linking contractile
functions of muscle sarcomeres to membrane systems such as the
sarcoplasmic reticulum or the T-tubules associated with excitation–
contraction coupling
2,8
.
The very N-terminal region of titin comprises a domain topology
that has been predicted to consist of two immunoglobulin-like
domains, referred to as Z1 and Z2 (ref. 9). Co-localization studies,
two-hybrid interaction screens and pull-down assays have demon-
strated that they interact with the N-terminal region of telethonin at
the Z-disk periphery
3,4
. However, although the interaction with
telethonin has been considered as a ‘cap’ (hence the alternative
name ‘T-cap’), or a ‘bolt’
3
, it is not known how titin–telethonin
binding affects the overall architecture of myofibrils and their
associated functions. The physiological importance of this inter-
action has been supported by evidence linking mutations in the
N-terminal regions of titin, telethonin and the telethonin-binding
site of muscle LIM protein (MLP) to different familial forms of
limb-girdle muscular dystrophy, as well as hypertrophic and dilated
cardiomyopathy
10–12
. These findings, together with complementary
data from animal models, indicate the possible existence of a link
between the titin–telethonin–MLP interaction and mechanical stress
sensor pathways
10
.
Depending on the specific isoform of titin, 200–700 N-terminal
residues of multimeric titin filaments are located within and cross
over most of the Z-disk of striated muscle sarcomeres
2,3,6
. However,
no data are yet available on the molecular nature of the titin–titin
association. Here we have determined the crystal structure of its
N-terminal region in complex with the titin-binding domain of
telethonin (Fig. 1, Table 1 and Supplementary Fig. S1). The latter
domain is sufficient to localize telethonin to the Z-disk of cardiac
myofibrils (Supplementary Fig. S2). Contrary to previous expec-
tations
3
and previous structural findings on other immunoglobulin-
like domain-containing proteins (see Supplementary Information),
our data reveal an antiparallel assembly of two titin molecules
mediated by telethonin, indicating that telethonin might have a
key role in titin assembly and Z-disk anchoring.
In the complex, the two N-terminal immunoglobulin-like
domains of titin, Z1 and Z2 are in an extended conformation and
are connected by a short three-residue linker. The two domains have
similar structures (root-mean-square deviation (r.m.s.d.) ¼ 0.66 A
˚
,
for all common main-chain atoms) and sequences (40 of 98 residues
are identical). In each of the two titin molecules, domains Z1 and Z2
are almost equally translated by 48 A
˚
and rotated by 538 and 618 with
respect to each other, generating a superhelical coil arrangement of
each titin N terminus. The second component of the complex,
telethonin, forms a unique elongated structure with a central
five-stranded antiparallel b-sheet that is extended by two exposed
LETTERS
Table 1 | Refinement statistics
Resolution (A
˚
) 15.0–2.45
R
work
/R
free
(%) 23.2/26.5
Number of atoms
Protein 3,726
Ion 25
Water 179
B factors (A
˚
2
)
Protein 49.7
Ion 51.2
Water 48.6
R.m.s.d.
Bond lengths (A
˚
) 0.011
Bond angles (8) 1.370
1
EMBL-Hamburg c/o DESY, Notkeststrasse 85, D-22603 Hamburg, Germany.
2
Institute of Physical Chemistry, National Center for Scientific Research ‘Demokritos’, Aghia
Paraskevi 15310, Athens, Greece.
3
The Randall Division of Cell and Molecular Biophysics and Cardiovascular Division, King’s College London, Guy’s Campus, London SE1 1UL, UK.
4
Institute of Cell Biology, ETH Zurich Hoenggerberg, CH-8093 Zurich, Switzerland.
5
Biozentrum, University of Basel, Division of Structural Biology, Klingelbergstrasse 70,
CH-4056 Basel, Switzerland.
*These authors contributed equally to this work.
Vol 439|12 January 2006|doi:10.1038/nature04343
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