Case Report
Effectiveness of Bortezomib in Cardiac AL Amyloidosis:
A Report of Two Cases
Santi Nigrelli,
1
Giuseppe Curciarello,
2
Piercarlo Ballo,
3
Stefano Michelassi,
1
and Francesco Pizzarelli
1
1
Department of Medicine, Nephrology Unit, St. M. Annunziata Hospital, ASL 10, Florence, Italy
2
Hematology and Transfusional Service, St. M. Annunziata Hospital, ASL 10, Florence, Italy
3
Cardiology Unit, St. M. Annunziata Hospital, ASL 10, Florence, Italy
Correspondence should be addressed to Santi Nigrelli; nigrellisanti@hotmail.com
Received 6 October 2013; Revised 3 February 2014; Accepted 5 February 2014; Published 10 March 2014
Academic Editor: Michael S. Firstenberg
Copyright © 2014 Santi Nigrelli et al. his is an open access article distributed under the Creative Commons Attribution License,
which permits unrestricted use, distribution, and reproduction in any medium, provided the original work is properly cited.
Cardiac involvement is a major prognostic determinant in patients with primary AL amyloidosis. he clinical results of standard
therapeutic approaches are suboptimal. It has been recently shown that bortezomib, an inhibitor of the proteasome, can induce rapid
favourable responses in AL amyloidosis improving cardiac function and survival. Herein we report on two patients with cardiac
amyloidosis treated by bortezomib who experienced partial or total remission of hematologic disease and of cardiac involvement.
However, death of one patient, sufering from chronic kidney disease stage 5, due to fulminant respiratory syndrome suggests the
need for caution in bortezomib use if patients have this comorbid condition.
1. Introduction
Cardiac amyloidosis, which occurs as a complication of
primary amyloidosis, is a result of cardiac deposition of insol-
uble, monoclonal immunoglobulin light chain fragments.
his is observed in about 50% of patients with light chain
amyloidosis predominantly ater 40 years of age with higher
prevalence in men than in women. he development of
restrictive cardiomyopathy, complicated by progressive let
ventricular or biventricular dysfunction, represents a major
determinant of adverse outcome for these patients who
typically die as a result of progressive heart failure or sudden
cardiac death.
A simple staging index for cardiomyopathy, based on
levels of N-terminal brain natriuretic peptide (NTproBNP)
and troponin I at presentation of disease, has been shown to
predict median survival of 27.2, 11.1, and 4.1 months in stages I
(normal values of both markers), II (altered values of only one
marker), or III (altered values of both markers), respectively
[1].
he aim of cardiac amyloidosis treatment is to reduce the
concentration of the amyloidogenic light chains and to induce
improvement of cardiac function and survival [2, 3] and it is
crucial that treatment is rapidly efective, tolerable, and safe.
he severity of cardiac involvement and the high tox-
icity treatment proile, however, have always limited the
outcome of traditional treatment options based on high dose
melphalan chemotherapy followed by autologous stem cell
transplantation.
Recently it has been shown that bortezomib, a proteasome
inhibitor, can induce rapid responses in AL amyloidosis
improving cardiac function and survival [4].
We report herein two cases of cardiac amyloidosis in
which treatment with bortezomib was associated with partial
or complete clinical remission of disease.
2. Case Presentation
2.1. Case Report 1. A 54-year-old man was referred to our
institution in June 2006 because of clinical signs of congestive
heart failure.
He was a long distance runner and diver but during the
last year he had experienced progressive dyspnea and fatigue
in his sport activities.
Hindawi Publishing Corporation
Case Reports in Medicine
Volume 2014, Article ID 627474, 6 pages
http://dx.doi.org/10.1155/2014/627474