Citation: Ghannam A, Germenis AE and Drouet C. Hereditary Kinin-Mediated Angioedema: Current Challenges.
Austin Intern Med. 2016; 1(1): 1002.
Austin Intern Med - Volume 1 Issue 1 - 2016
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Ghannam et al. © All rights are reserved
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desArg
9
-Lys-BK. hese vasoactive peptides, BK, Lys-BK and their
metabolites desArg
9
BK, and desArg
9
-Lys-BK interact with G-coupled
protein receptors B2R and B1R. Local angioedema attacks depend
on the local receptor expression, in particular B1R in inlammatory
conditions and its activation by agonists desArg
9
-BK and desArg
9
-
Lys-BK.he potency of these agonists to stimulate B1R is not relected
by ainity. B1R agonists are with suicient concentration and with
long half-life enough to stimulate B1R [6]. Besides, the agonistic
activity of desArg
9
-BK for B1R is enhanced by CPM [7].
he main enzyme for desArg
9
-BK catabolism is Aminopeptidase
P (APP); its activity in C1-Inh deicient patients’ plasma, inversely
correlate with disease severity, supporting a role for desArg
9
-BK
in HAE attacks [8]. On the other hand, in FXII-HAE patients, the
severity inversely correlate with ACE and CPN activity rather than
with APP levels [9].
As far as the genetics of angioedema is considered [10], the main
discovery made at the turn of the century is that C1-Inh deiciency
is not the only cause of HAE. Cases of inherited angioedema with
normal plasma levels of fully functional C1-Inh and without causal
mutations at the SERPING1 locus (nlC1-Inh-HAE) are recognized
increasingly oten, especially amongst patients sufering from
estrogen-associated HAE. Nearly a tenth of nlC1-Inh-HAE cases
could be attributed to gain-of-function mutations in the gene
encoding the coagulation Factor XII (F12) [11]. Interestingly and
on the contrary to the uniform C1-Inh-HAE epidemiology around
the world, FXII-HAE seems to be prevalent in certain areas, a fact
indicating that the responsible F12 mutations may represent a
founder efect. In any case, this discovery signiies that the genetic
basis of HAE is far from being completely understood. Since isolated
or combined deiciencies in enzymes involved in kinin degradation
(carboxypeptidase N, angiotensin-I converting enzyme, APP) have
been detected in various forms of kinin-mediated angioedema [12],
it is not improbable that in the future, causative alterations in genes
other than SERPING1 and F12, will be detected.
Moreover, accumulating evidence indicates that functional
mutations in genes encoding proteins involved in kinin metabolism
and/or function are associated with the severity of C1-Inh-HAE or
with the emergence of acquired angioedema. Should these indings
will be conirmed, they will explain, at least partially, the enormous
clinical heterogeneity of the disease observed even among members
of the same family sharing the same SERPING1 causative mutation.
Generally, the better understanding of these associations will help to
develop strategies to deal with their implications for the individual
patient.
Besides, in about 5% of C1-Inh-HAE cases, no mutation can be
detected in the coding region of SERPING1.But the fact that almost
all sufering heterozygotes present with plasma C1-Inh concentration
Editorial
Firstly described in 1882 by Heinrich Quincke, angioedema was
regarded for more than one century as a rare disease [1]. Subsequently,
it was established that the hereditary form of the disease (Hereditary
Angioedema, HAE) is caused by a deiciency of C1-Inhibitor (C1-
Inh) [2] due to alterations in the encoding SERPING1 gene [3] and
Bradykinin (BK) was recognized as the principal mediator of HAE
symptoms [4]. Over the past decade, however, impressive research
advances uncovered an astonishing complexity of the disease. As
a result, nowadays, kinin-mediated angioedema is considered as
adverse family of disorders, whose the only common characteristics
is an unpredictable clinical expression by spontaneous, recurrent,
self-limiting but potentially life-threatening attacks of localized
edema of subcutaneous and submucosal tissues. hereater, a series
of challenging pathophysiological and genetic aspects of the disease
that remain to be deciphered, are continuously revealed.
Angioedema attacks result from an increased vasopermeability
that is induced by the generation of BK through a local process
precipitated by systemic contact system activation. Convincing
evidence about the systemic kinin formation is that swellings during
a given angioedema attack can occur at multiple sites, as well as that
inhibitors able to control kallikrein activity reduce vasopermeability
and attack severity [5].
C1-Inh is the major control of contact phase proteases, targeting
kallikrein and FXIIa. It plays a role in regulating its systemic,
luid-phase activation, and in preventing dissemination of contact
activation process. herefore, C1-Inh deiciency is associated with
uncontrolled contact phase activation and, subsequently, with
generation of vasoactive peptides, BK and its active metabolite
desArg
9
-BK ater being processed by carboxypeptidases N/M. Another
kinin, called kallidin (Lys-BK), can be produced from low molecular
weight kininogen. Lys-BK is transformed by carboxypeptidases into
Editorial
Hereditary Kinin-Mediated Angioedema: Current
Challenges
Ghannam A
1,2
*, Germenis AE
3,4
and Drouet C
1,5
1
GREPI (Group for Research and Study of Inlammatory
Processes) EA7408, Universite Grenoble Alpes, France
2
KininX SAS, Grenoble, France
3
Department of Immunology & Histocompatibility,
University of Thessaly, Larissa, Greece
4
Department of Molecular Medicine, Hellenic Pasteur
Institute, Athene, Greece
5
Centre de Reference des Angioedemes CREAK, CHU
Grenoble Alpes, France
*Corresponding author: Arije Ghannam, KininX SAS,
Universite Grenoble Alpes, GREPI EA7408, EFS Rhone-
Alpes, PO Box 35, 29 Avenue Maquis du Gresivaudan,
F-38701 LA TRONCHE, France
Received: June 28, 2016; Accepted: June 29, 2016;
Published: June 30, 2016