Introduction
Breast cancer is a heterogeneous disease with diverse morpholo-
gies, molecular characteristics, clinical behavior, and response to
therapeutics. As we delve more into the complex nature of this
disease, it becomes imperative to determine appropriate prog-
nostic and predictive markers that can be used by physicians and
patients for informed decision making. The concept of personalized
medicine recognizes this heterogeneity and considers each patient
as having a unique tumor. Under this new paradigm, the cancer
community foresees the possibility of predictive and prognostic
parameters associated with recurrence and/or response to specific
therapies that are unique to each individual. This review summa-
rizes the various tools used for prognostication in breast cancer, the
developing methods, and speculates on the characteristics necessary
for an “ideal” future tool.
Classic Prognostic Tools
The most important prognostic markers for any cancer are
tumor size, lymph node status, and histologic features, and this
is no different for breast cancer.
1
Tumor size and nodal status are
time-dependent variables and reflect the duration for which the
tumor has been present. Tumor size is a good prognostic marker for
distant relapse in lymph node–negative patients.
2,3
However, even
patients with small tumors (< 1 cm) have a 12% chance of recur-
rence.
4,5
In addition, tumor size measurement is confounded by
several factors such as stromal desmoplastic reaction, coexisting in
in situ lesions and tumor multicentricity.
6
Nodal status is predictive
of both disease-free and overall survival.
7-9
In addition, the number
of positive lymph nodes directly predicts survival.
2,6
However, 30%
of node-negative patients still develop recurrences by 10 years.
6
Histologic classification is the morphologic assessment of inva-
sive carcinomas for the degree of differentiation and the “proxim-
ity of resemblance” to normal tissue.
1
There are 2 components
to histologic classification: type and grade.
1,10
The predominant
type, invasive ductal of no special type, accounts for up to 75%
of all breast cancers; this significantly limits the use of type as a
prognostic factor.
1,10
Grade provides a qualitative assessment of
the biologic characteristics of the tumor; eg, high-grade tumors
behave aggressively and have poor prognosis while low grade
tumors have better prognosis.
11-14
However, there is only a modest
Abstract
Personalized Medicine: The Road Ahead
Rutika Mehta, Rohit K. Jain, Sunil Badve
With breast cancer now being recognized as a heterogeneous disease, the concept of personalized medicine de-
mands that the tumor of every individual be treated uniquely. This has lead to ever-expanding use of existing prognos-
tic and predictive markers, and the search for better ones is ongoing. The classic prognostic tools such as tumor size,
lymph node status, grade, hormone receptors, and HER2 status are now supplemented by gene expression–based
tools such as PAM50 and MammaPrint. However, the overdependence of these tools on proliferation-related genes
is a signiicant handicap. Although pathway-based signatures hold great promise in future breast cancer prognos-
tication, the fact that every tumor has multiple functional pathways signiicantly limits the utility of this approach.
Developed by the integration of estrogen receptor (ER), HER2, proliferation-related, and other genes, the Oncotype
DX assay has been able to provide valuable prognostic information for ER-positive tumors. Newer molecular markers
based on cancer stem cells, single-nucleotide polymorphisms (SNPs), and miRNAs are becoming available, but their
importance needs to be validated. It is clear that breast cancer is a multifaceted process and that none of the tools
can reliably predict a binary outcome (recurrence or no recurrence). The breast cancer community is still awaiting
an ideal prognostic tool that can integrate knowledge from classic variables such as tumor size and grade with new
throughput technology and principles of pharmacogenomics. Such a tool will not only deine prognostic subgroups
but also be able to predict therapeutic eficacy and/or resistance based on molecular proiling.
Clinical Breast Cancer, Vol. 11, No. 1, 20-26, 2011; DOI: 10.3816/CBC.2011.n.004
Keywords: Future directions, Prognostic factors
Review
Department of Pathology, Indiana University School of Medicine, Indianapolis
Submitted: Jun 29, 2010; Revised: Aug 16, 2010; Accepted: Aug 18, 2010
Address for correspondence: Sunil Badve, MD, FRCPath, Department of Pathology,
Indiana University School of Medicine, 350 W 11th Street, IUHPL 4050,
Indianapolis, IN 46202
Fax: 317-491-6419; e-mail: sbadve@iupui.edu
1526-8209/$ - see frontmatter
© 2011 Elsevier Inc. All rights reserved.
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Clinical Breast Cancer February 2011
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