Analgesic -Conotoxins CVIE and CVIF Selectively and Voltage-Dependently Block Recombinant and Native N-Type Calcium Channels G. Berecki, 1 L. Motin, A. Haythornthwaite, S. Vink, P. Bansal, R. Drinkwater, C. I. Wang, M. Moretta, R. J. Lewis, P. F. Alewood, M. J. Christie, and D. J. Adams 2 The Queensland Brain Institute (G.B., L.M., D.J.A.), the School of Biomedical Sciences (G.B., A.H., D.J.A.), and Institute for Molecular Bioscience (S.V., P.B., C.I.W., R.J.L., P.F.A.), the University of Queensland, Queensland, Australia; Xenome Ltd., Indooroopilly, Queensland, Australia (R.D.); and Brain and Mind Research Institute, University of Sydney, New South Wales, Australia (M.M., M.J.C.) Received June 24, 2009; accepted October 23, 2009 ABSTRACT Neuronal (N)-type Ca 2+ channel-selective -conotoxins have emerged as potential new drugs for the treatment of chronic pain. In this study, two new -conotoxins, CVIE and CVIF, were discovered from a Conus catus cDNA library. Both conopeptides potently displaced 125 I-GVIA binding to rat brain membranes. In Xenopus laevis oocytes, CVIE and CVIF potently and selectively inhibited depolarization- activated Ba 2+ currents through recombinant N-type (1 B-b / 2 1/ 3 ) Ca 2+ channels. Recovery from block increased with membrane hyperpolarization, indicating that CVIE and CVIF have a higher affinity for channels in the inactivated state. The link between inactivation and the reversibility of -cono- toxin action was investigated by creating molecular diversity in subunits: N-type channels with 2a subunits almost completely recovered from CVIE or CVIF block, whereas those with 3 subunits exhibited weak recovery, suggesting that reversibility of the -conotoxin block may depend on the type of -subunit isoform. In rat dorsal root ganglion sensory neurons, neither peptide had an effect on low-voltage- activated T-type channels but potently and selectively inhib- ited high voltage-activated N-type Ca 2+ channels in a volt- age-dependent manner. In rat spinal cord slices, both peptides reversibly inhibited excitatory monosynaptic trans- mission between primary afferents and dorsal horn superfi- cial lamina neurons. Homology models of CVIE and CVIF suggest that -conotoxin/voltage-gated Ca 2+ channel inter- action is dominated by ionic/electrostatic interactions. In the rat partial sciatic nerve ligation model of neuropathic pain, CVIE and CVIF (1 nM) significantly reduced allodynic behav- ior. These N-type Ca 2+ channel-selective -conotoxins are therefore useful as neurophysiological tools and as potential therapeutic agents to inhibit nociceptive pain pathways. Neuronal (N)-type voltage-gated calcium channels (VGCCs) play important roles in regulating neuronal excitability and nociceptive transmission and are prominently involved in the transduction of acute and chronic pain perception (Snutch, 2005; Yasuda and Adams, 2007). These channels represent important drug targets for the management of chronic and neuropathic pain and have been investigated in the develop- ment of new analgesic agents (McGivern, 2006; Schroeder et al., 2006). A number of structurally related -conopeptides of the genus Conus (cone snails) selectively inhibit N-type VGCCs of pain-sensing primary nociceptors (Olivera et al., 1994). Among these, the -conotoxin MVIIA (ziconotide) still maintains its orphan drug status as a valuable alternative intrathecal analgesic for the management of chronic intrac- table pain, especially in patients refractory to opioids (Klotz, 2006). Other conopeptides, such as CVID, are currently in clinical trials (McGivern, 2006) and hold promise for the This work was supported by the National Health and Medical Research Council Program [Grant 351446]; and a University of Queensland Postdoctoral Research Fellowship. 1 Current affiliation: Department of Physiology and Pharmacology, Hotch- kiss Brain Institute, University of Calgary, Calgary, Alberta, Canada. 2 Current affiliation: Health Innovations Research Institute, Royal Mel- bourne Institute of Technology University, Bundoora, Victoria, Australia. Article, publication date, and citation information can be found at http://molpharm.aspetjournals.org. doi:10.1124/mol.109.058834. ABBREVIATIONS: VGCC, voltage-gated calcium channel; CVID, -conotoxin CVID; CVIE, -conotoxin CVIE; CVIF, -conotoxin CVIF; DRG, dorsal root ganglion; EPSC, excitatory postsynaptic current; HP, holding potential; PNL, partial nerve ligation; HPLC, high-performance liquid chromatography; RP-HPLC, reversed-phase high-performance liquid chromatography; PCR, polymerase chain reaction; ANOVA, analysis of variance; BAPTA, 1,2-bis(2-aminophenoxy)ethane-N,N,N',N'-tetraacetic acid; TFA, trifluoroacetic acid; N, neuronal; SNX-331, Y13W derivative of -conotoxin MVIIC. 0026-895X/10/7702-139–148$25.00 MOLECULAR PHARMACOLOGY Vol. 77, No. 2 Copyright © 2010 The American Society for Pharmacology and Experimental Therapeutics 58834/3551986 Mol Pharmacol 77:139–148, 2010 Printed in U.S.A. 139 at RMIT Library Serials on April 15, 2012 molpharm.aspetjournals.org Downloaded from http://molpharm.aspetjournals.org/content/80/2/356.full.pdf An erratum has been published: