Clinical Trial of 0.02% Polyhexamethylene Biguanide Versus Placebo in the Treatment of Microsporidial Keratoconjunctivitis SUJATA DAS, SRIKANT K. SAHU, SAVITRI SHARMA, SHYAM SUNDAR NAYAK, AND SARITA KAR PURPOSE: To evaluate the efficacy of 0.02% polyhexa- methylene biguanide (PHMB) in the treatment of kera- toconjunctivitis caused by microsporidia. DESIGN: Prospective, double-masked, randomized, pla- cebo-controlled clinical trial. METHODS: One hundred forty-five patients in a single- center, institutional setting were recruited. Patients with superficial keratoconjunctivitis and corneal scrapings with positive results for microsporidial spores were in- cluded. Patients with any known allergy to PHMB, and clinically suspected bacterial, viral, or fungal infection were excluded from the study. One hundred forty-five patients were treated at 4-hour intervals with either topical 0.02% PHMB (n 72) or placebo (n 73). The patients were followed-up on day 3 1, day 7 1, and weekly thereafter, until complete resolution of the cor- neal lesions. Patients with deterioration of clinical symp- toms and signs were removed from the study and were treated with PHMB. Main outcome measures included resolution time, cure time, and final visual outcome. RESULTS: Resolution time was defined as the amount of time until disappearance of corneal epithelial infil- trates. Cure time was defined as the interval until absence of conjunctival congestion, corneal epithelial lesion, and superficial punctate keratitis. Baseline characteristics showed no relevant difference between the groups. The mean resolution time was 4.9 2.2 days and 4.6 2.3 days in the PHMB and placebo groups, respectively (P .49). The mean time for cure was 13.5 6.6 days and 9.4 5.1 days in PHMB and placebo groups, respec- tively (P .004). There was no significant difference in the final visual outcome between the groups (P .10). No serious adverse effects were noted. CONCLUSIONS: Treatment of microsporidial kerato- conjunctivitis with PHMB does not offer any significant advantage over placebo, suggesting self-limiting nature of the disease. (Am J Ophthalmol 2010;150:110 –115. © 2010 by Elsevier Inc. All rights reserved.) M ICROSPORIDIA ARE SMALL, OBLIGATE, SPORE- forming, intracellular living eukaryotes that infect a broad range of vertebrates and inver- tebrates. 1 In humans, microsporidia are opportunistic pathogens that are reported to cause gastrointestinal, sinus, pulmonary, muscular, renal, and ocular disease. The ocular manifestations include superficial keratoconjunctivitis and stromal keratitis. 2 The early reports of microsporidial keratoconjunctivitis involved immunocompromised pa- tients. 3–6 However, these pathogens seem to be increas- ingly prevalent in immunocompetent patients. 7–10 We have reported an epidemic of keratoconjunctivitis caused by microsporidia. 9 The management of microsporidial keratoconjuncti- vitis is challenging because no definitive treatment exists. Anecdotal reports of specific treatment include the use of albendazole, 8,11 broad-spectrum antibiotics, 7,8 itraconazole, 10,12 propamidine isoethionate, 6,13 fumagil- lin, 3,5,14 chlorhexidine, 7 polyhexameththylene biguanide, 7 and lubricants. 3 In all studies, epithelial keratoconjuncti- vitis has been reported to resolve in a varying period without significantly affecting visual acuity. The present study was designed to determine the clinical efficacy of 0.02% polyhexameththylene biguanide (PHMB) in the treatment of keratoconjunctivitis caused by microsporidia. METHODS THIS SINGLE-CENTER, DOUBLE-MASKED, RANDOMIZED, PLA- cebo-controlled clinical trial examined 145 patients. In- formed written consent was obtained from each participant before inclusion in the study. INCLUSION AND EXCLUSION CRITERIA: Patients with superficial epithelial keratitis or keratoconjunctivitis and whose corneal scrapings showed positive results for micros- poridia spores were included in the study. The patients needed to have the ability to understand and sign an informed consent form. For patients younger than 18 years, the informed consent was required to be understood and signed by the parent or guardian. The exclusion criteria included known allergy to PHMB and clinically suspected bacterial, viral, or fungal infection of the cornea. Accepted for publication Jan 29, 2010. From the Cornea and Anterior Segment Service (S.D., S.K.S., S.S.N.) and the Ocular Microbiology Service (S.S., S.K.), L. V. Prasad Eye Institute, Bhubaneswar, Orissa, India. Inquiries to Savitri Sharma, Ocular Microbiology Service, L. V. Prasad Eye Institute, Bhubaneswar, Orissa, India 751024; e-mail: savitri@ lvpei.org © 2010 BY ELSEVIER INC.ALL RIGHTS RESERVED. 110 0002-9394/$36.00 doi:10.1016/j.ajo.2010.01.038