HDACInhibitorsandCardiacSafety
InResponse: In response to the Editorial (1) published
aboutourarticleentitled‘‘Cardiotoxicityofhistonedeacetylase
inhibitor depsipeptide in patients with metastatic neuroendo-
crinetumors’’(2)andinresponsetotheLettertoEditorinthis
issuebyMolifeetal.,wemakethefollowingpoints:
1.Fourofthesixseriouscardiacadverseeventswereported
met the definition of serious adverse event by the common
terminology criteria for adverse events as follows: one patient
had sudden death; one patient with grade 2 prolonged QTc
(QTc of 499 ms) was hospitalized for close monitoring of
cardiac arrhythmia; and two patients developed ventricular
tachycardiaforwhichhospitalizationwasprolonged.Although
we used ‘‘serious cardiac adverse events’’ eight times in our
article,thiswasprecededseventimesbytheterm‘‘potential’’to
underscore that prolonged QTc or ventricular tachycardia
potentially could result in serious outcome.
In general, the common terminology criteria for adverse
events grading classifies mild, moderate, severe, and life-
threateningadverseeventsasgrade1,2,3,and4,respectively.
However,eachadverseeventneedstobeassessedinthecontext
of specific clinical settings. For example, grade 2 neutropenia
(neutrophil counts between 1,000/mm
3
and 1,500/mm
3
)may
pose different risk than grade 2 ventricular arrhythmia (e.g.,
torsade de pointes requiring nonurgent medical intervention).
Similarly,aQTcintervalof499ms(grade2)maybeasriskyas
havingaQTcof501ms(grade3).
2. On the aggregate, our group has broad experience and
expertise in oncology drug development and has played a
criticalroleinsalvagingandoptimizingtheuseofseveraldrugs
(e.g.,flavopiridol,pentostatin,fludarabine,andrituximab)that
are now in the advanced stages of clinical trials or routinely
used as standard of care. Additionally, we have been active in
reporting many toxicities associated with common oncology
drugs. Similarly, our group has a decade-long experience
working with depsipeptide both preclinically and clinically
(3–7);thus,inthepast,wehavebeenverycommittedtothe
clinicaldevelopmentofthiscompound.Ourmostrecentreport
wasintendedtoaccuratelyconveyourfindings.Inouropinion,
six sudden deaths reported in f450 patients treated with
depsipeptideinearly-phaseclinicaltrialsisalarmingregardless
of the underlying patient risk factors for sudden death. Such
results indicate that despite extensive preclinical and phase I
clinicaltrialexperience,wehavenotyetidentifiedspecificrisk
factorsforsuddendeaththatmayberelatedtothisagent.This
is a particularly important point given that other therapeutic
compoundswithinthesameclassofdrugsofdepsipeptidemay
lack this unacceptable toxicity. We never suggested ‘‘abandon-
ing’’ this class of agents as stated in the Editorial, but stressed
thatcontinuedevaluationoftheseagentsbepursuedtoidentify
risks associated with cardiotoxicity.
3.Afterweighingtherisktobenefitratiotoourpatients,we
collectively decided to terminate the phase II depsipeptide
study in patients with metastatic neuroendocrine cancers and
not to initiate additional studies with this agent in leukemia
and lymphoma. Given the enormous potential histone
deacetylase inhibitors have in oncology, we do believe that
furtherstudiestolearnfactorspredisposingtouncommonbut
fatal events are of great importance. It is the process of
identifying, reporting, and learning the management of
toxicities of several chemotherapeutic agents that has allowed
us to use most of the oncology drugs effectively in the clinic
today. However, given that promising alternative agents
targeting histone deacetylase may lack the risk of sudden
cardiac death as an unpredicted rare toxicity are currently
availableforclinicalinvestigation,wehavechosentofocuson
alternativehistonedeacetylaseinhibitorsinourpreclinicaland
clinical studies at The Ohio State University.
Manisha H. Shah
Miguel A. Villalona-Calero
Guido Marcucci
John C. Byrd
Michael R. Grever
Ohio State University,
Columbus, Ohio
References
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F 2007AmericanAssociationforCancerResearch.
doi:10.1158/1078-0432.CCR-06-2380
Letters to the Editor
www.aacrjournals.org ClinCancerRes2007;13(3)February1,2007 1068
Research.
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