International Journal of Contemporary Pediatrics | January 2020 | Vol 7 | Issue 1 Page 212
International Journal of Contemporary Pediatrics
Nandy A et al. Int J Contemp Pediatr. 2020 Jan;7(1):212-216
http://www.ijpediatrics.com pISSN 2349-3283 | eISSN 2349-3291
Case Report
Deviation of paradigmatic mutations found in
shprintzen-goldberg syndrome
Arnab Nandy*, Sankar K. Das, Sumit Roy, Shreyasi Das
INTRODUCTION
Shprintzen-Goldberg (S-G) Syndrome recognized as a
rare congenital connective tissue disorder characterized
by craniofacial dysmorphism, craniosynostosis, and
multisystem abnormalities.
1
Although craniosynostosis
and marfanoid habitus known as common expression
here yet a wide variety of phenotypic presentations could
be noticed.
2,3
Often S-G syndrome mimic Marfan
syndrome and Loeys-Dietz syndrome owing to their
phenotypic overlapping.
4
Considering the rarity, S-G
syndrome being primarily diagnosed with its’ clinical
features as genetic basis of the condition observed to be
deciphered gradually over time.
5
So far, autosomal
dominant pattern of inheritance and sporadic incidences
being reported for S-G syndrome where germline
mutations which considered to be responsible for
dysregulation of TGF-β cytokine during embryogenesis
leading to such phenotypic presentation.
6
A patient with
similar condition was evaluated where conventionally
reported mutations were found to be absent.
CASE REPORT
A five-months old male infant was evaluated for
congenital connective tissue disorder, initially presented
with dysmorphic craniofacial features and developmental
delay although ante-natal and perinatal history were
insignificant. The infant was born full-term AGA with
normal birth weight and recorded to have natal teeth and
empty scrotal sac at birth. His elder male sibling was
doing well. On examination, fused sagittal suture,
ABSTRACT
Shprintzen-Goldberg (S-G) Syndrome known as rare congenital connective tissue disorder where craniosynostosis
and marfanoid habitus found to be the usual presentation. Craniofacial dysmorphism with multi-organ involvement
documented to be amongst prominent features of this syndrome. Case characteristics is five-month-old male infant
with craniosynostosis, and motor developmental delay was evaluated for congenital connective tissue disorder.
Dysmorphic craniofacial features like dolichocephaly, triangular forehead, ocular hypertelorism, micrognathia and
retrognathia were noticed besides congenital umbilical hernia, empty scrotal sac, clinodactyly with long slender
fingers, hyper-mobile joints, hypotonia. Subsequent investigations revealed normal male karyotype (46, XY) while
genetic analysis depicted missense mutations in six different genes. Conventionally, mutation in SKI gene reported
for its’ associated with S-G syndrome where dysregulation of TGF-β signaling was discussed as the primary reason.
In the present case discussed here, it was found to have polygenic mutational association where few novel genetic
mutations were seen.
Keywords: Craniofacial abnormality, Craniosynostosis, Germline mutation, Marfanoid habitus, Shprintzen-Goldberg
Craniosynostosis syndrome, Undescended testis
Department of Paediatric Medicine, North Bengal Medical College, Darjeeling, West Bengal, India
Received: 03 October 2019
Revised: 04 November 2019
Accepted: 11 November 2019
*Correspondence:
Dr. Arnab Nandy,
E-mail: arnabn.office@gmail.com
Copyright: © the author(s), publisher and licensee Medip Academy. This is an open-access article distributed under
the terms of the Creative Commons Attribution Non-Commercial License, which permits unrestricted non-commercial
use, distribution, and reproduction in any medium, provided the original work is properly cited.
DOI: http://dx.doi.org/10.18203/2349-3291.ijcp20195756