World J Pediatr, Vol 5 No 2
.
May 15, 2009
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www.wjpch.com
93
Update on disorders of sex development
Review article
Author Affiliations: Department of Pediatrics, Division of Pediatric
Endocrinology, University Hospital Gent, De Pintelaan 185, 9000 Gent,
Belgium (Cools M); Department of Pathology, Erasmus Medical Center,
Josephine Nefkens Institute, Daniel Den Hoed Cancer Clinic, Postbus
2040, 3000 DR Rotterdam, The Netherlands (Looijenga LHJ); Department
of Urology (Wolffenbuttel KP) and Department of Pediatrics (Drop SLS),
Sofia Children's Hospital, Dr Molewaterplein 60, 3015 GJ Rotterdam, The
Netherlands
Corresponding Author: Martine Cools, Department of Pediatrics, Division
of Pediatric Endocrinology, University Hospital Gent, Building 5K6, De
Pintelaan 185, 9000 Gent, Belgium (Tel: +32 93324728; Email: martine.
cools@ugent.be)
doi:10.1007/s12519-009-0020-7
©2009, World J Pediatr. All rights reserved.
Background: Considerable progress has been made
on genetic mechanisms involved in disorders of sex
development and on tumor formation in dysgenetic
gonads. Clinical and psychological outcome of patients
are, as far as evaluated, unsatisfactory at present.
Guidelines are emerging in order to optimize long-term
outcome in the future.
Data sources: The information obtained in this review
is based on recent original publications and on the
experience of our multidisciplinary clinical and research
group.
Results: This review offers an update on our knowledge
concerning gene mutations involving in disorders of
sex development, on the renewed nomenclature and
classification system, and on the mechanisms of tumor
development in patients.
Conclusions: The consensus meeting on disorders
of sex development has renewed our interest in clinical
studies and long-term outcome of patients. Psychological
research emphasizes the importance to consider male
gender identity wherever possible in cases of severe
undervirilization. Patient advocacy groups demand a
more conservative approach regarding gonadectomy.
Medical doctors, scientists and governmental instances
are increasingly interested in the set-up of international
research collaborations. As a consequence, it is expected
that new guidelines for the optimal care of patients will be
proposed in the coming years.
World J Pediatr 2009;5(2):93-102
Key words: consensus;
germ cell tumor;
nomenclature;
risk;
sex development
Introduction
D
isorders of sex development (DSD) is
regarded as an umbrella term, referring to
a group of congenital conditions in which
the development of the chromosomal, gonadal or
anatomical sex has been atypical.
[1,2]
DSD has replaced
the formerly used term "intersex".
DSD represents a markedly heterogeneous group
of conditions. On one hand, identical genetic defects
may result in various clinical presentations; on the
other hand, a similar phenotype may be the end point
of different genetic pathways. A detailed insight in the
stepwise normal process of sex development and the
different genes involved is essential to understand the
mechanisms eventually leading to DSD.
Specific subgroups of DSD patients are prone to
the development of a germ cell tumor (GCT). Their
individual risk profile can be estimated by combining
knowledge on the specific gonadal differentiation
patterns present in patients, and detailed histological
and genetic diagnostic investigations.
The process of normal sex development
The embryonic precursors of the gonads and genital
structures are bipotential, in other words, they have
the potential to differentiate either into the male or
female direction, depending on the correct and timely
expression of specific genes. In mammals, male sex
Martine Cools, Leendert HJ Looijenga, Katja P Wolffenbuttel, Sten LS Drop
Ghent, Belgium and Rotterdam, The Netherlands
Disorders of sex development: update on the genetic
background, terminology and risk for the
development of germ cell tumors