Original Paper Pancreatology 2005;5:354–360 DOI: 10.1159/000086535 Mutations in the Serine Protease Inhibitor Kazal Type 1 (SPINK1) Gene in Japanese Patients with Pancreatitis Kiyoshi Kume a Atsushi Masamune a Hiroya Mizutamari a Kenzo Kaneko a Kazuhiro Kikuta a Masahiro Satoh a Kennichi Satoh a Kenji Kimura a Noriaki Suzuki a Yutaka Nagasaki a Akira Horii b Tooru Shimosegawa a a Division of Gastroenterology, and b Department of Molecular Pathology, Tohoku University Graduate School of Medicine, Sendai, Japan higher in patients with familial pancreatitis (38 and 13%, respectively) and with idiopathic CP (13 and 16%) than normal subjects (0.6 and 0%). In addition, the frequency of [N34S; IVS1–37T 1 C] mutation was higher in patients with autoimmune CP (33%). Conclusion: The SPINK1 gene mutations were associated with pancreatitis also in Japan. Copyright © 2005 S. Karger AG, Basel and IAP Introduction Chronic pancreatitis (CP) is a progressive inflamma- tory disease that eventually leads to impairment of exo- crine and endocrine functions of the organ [1, 2]. The causes of CP are multifaceted. Most causes of CP have been attributed to alcohol abuse, in some cases hereditary or metabolic factors play a role, and the actual cause re- mains unknown in a substantial portion of the patients [1, 2]. Recent genetic studies have revealed an association between CP and mutations in the cationic trypsinogen (protease, serine, 1; PRSS1 ) gene [3–6], the serine prote- ase inhibitor Kazal type 1 ( SPINK1 , also called pancre- atic secretory trypsin inhibitor; PSTI ) gene [7–12], and the cystic fibrosis transmembrane conductance regulator gene [13, 14] . These genetic findings in CP supported the Key Words Pancreatitis Serine protease inhibitor Kazal type 1 Pancreatic secretory trypsin inhibitor Mutational analysis Familial pancreatitis Autoimmune pancreatitis Abstract Background/Aims: Recent studies have shown an asso- ciation between the N34S mutation in the serine prote- ase inhibitor Kazal type 1 (SPINK1) gene and chronic pan- creatitis (CP). We here examined the prevalence of SPINK1 mutations in Japanese patients with pancreati- tis. Methods: Genomic DNA was prepared from 80 Jap- anese patients with CP, 36 patients with acute pancreati- tis (AP), and 165 healthy controls. All exons and the promotor region of the SPINK1 gene were amplified by the polymerase chain reaction, and directly sequenced. Results: We found four types of mutation (N34S, IVS1– 37T 1 C, –215G 1 A, and IVS3 + 2T 1 C) and two types of polymorphism (–253T 1 C and 272C 1 T). The N34S muta- tion cosegregated with IVS1–37T 1 C, and was present in 8 CP and 1 AP patients. The –215G 1 A mutation was in a complete linkage with IVS3 + 2T 1 C, and was present in 8 CP and 1 AP patients. The prevalences of [N34S; IVS1– 37T 1 C] and [–215G 1 A; IVS3 + 2T 1 C] were significantly Received: October 6, 2003 Accepted after revision: May 11, 2004 Published online: June 23, 2005 Tooru Shimosegawa, MD, Division of Gastroenterology Tohoku University Graduate School of Medicine, 1-1 Seiryo-cho Aoba-ku, Sendai 980-8574 (Japan) Tel. +81 22 717 7171, Fax +81 22 717 7177 E-Mail tshimosegawa@int3.med.tohoku.ac.jp © 2005 S. Karger AG, Basel and IAP 1424–3903/05/0055–0354$22.00/0 Accessible online at: www.karger.com/pan Fax +41 61 306 12 34 E-Mail karger@karger.ch www.karger.com