cells
Review
Inducible Pluripotent Stem Cells as a Potential Cure for
Diabetes
Kevin Verhoeff
1,
* , Sarah J. Henschke
2
, Braulio A. Marfil-Garza
1
, Nidheesh Dadheech
3
and
Andrew Mark James Shapiro
4
Citation: Verhoeff, K.; Henschke, S.J.;
Marfil-Garza, B.A.; Dadheech, N.;
Shapiro, A.M.J. Inducible Pluripotent
Stem Cells as a Potential Cure for
Diabetes. Cells 2021, 10, 278. https://
doi.org/10.3390/cells10020278
Academic Editor: Adrian Kee
Keong Teo
Received: 1 January 2021
Accepted: 24 January 2021
Published: 30 January 2021
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4.0/).
1
Department of Surgery, University of Alberta, Edmonton, AB T6G 2B7, Canada; marfilga@ualberta.ca
2
Department of Emergency Medicine, University of Saskatchewan, Saskatoon, SK S7N 0W8, Canada;
shenschk@ualberta.ca
3
Alberta Diabetes Institute, University of Alberta, Edmonton, AB T6G 2B7, Canada; dadheech@ualberta.ca
4
FRCS (Eng) FRCSC MSM FCAHS, Clinical Islet Transplant Program, Alberta Diabetes Institute,
Department of Surgery, Canadian National Transplant Research Program, Edmonton, AB T6G 2B7, Canada;
jshapiro@ualberta.ca
* Correspondence: verhoeff@ualberta.ca; Tel.: +1-780-984-1836
Abstract: Over the last century, diabetes has been treated with subcutaneous insulin, a discovery that
enabled patients to forego death from hyperglycemia. Despite novel insulin formulations, patients
with diabetes continue to suffer morbidity and mortality with unsustainable costs to the health care
system. Continuous glucose monitoring, wearable insulin pumps, and closed-loop artificial pancreas
systems represent an advance, but still fail to recreate physiologic euglycemia and are not universally
available. Islet cell transplantation has evolved into a successful modality for treating a subset
of patients with ‘brittle’ diabetes but is limited by organ donor supply and immunosuppression
requirements. A novel approach involves generating autologous or immune-protected islet cells for
transplant from inducible pluripotent stem cells to eliminate detrimental immune responses and
organ supply limitations. In this review, we briefly discuss novel mechanisms for subcutaneous
insulin delivery and define their shortfalls. We describe embryological development and physiology
of islets to better understand their role in glycemic control and, finally, discuss cell-based therapies
for diabetes and barriers to widespread use. In response to these barriers, we present the promise of
stem cell therapy, and review the current gaps requiring solutions to enable widespread use of stem
cells as a potential cure for diabetes.
Keywords: islet cell transplant; diabetes; inducible pluripotent stem cells; immunosuppression;
immune reset; insulin
1. Insulin as a Treatment, Not a Cure
In 1889, Oskar Minkowski and Joseph von Mering completed a canine pancreatectomy
and induced fatal diabetes mellitus (DM). This experiment demonstrated the central role
of the pancreas in glycemic control [1]. In 1893, Williams and Harsant working in Bristol,
UK, attempted to transplant pancreatic fragments taken from a freshly slaughtered sheep
and placed them subcutaneously in a boy dying of diabetic ketoacidosis, with unsuccessful
results [2]. Even throughout the journey to discover insulin, Banting’s initial trials focused
on subcutaneous injection of an unpurified pancreatic slurry, and the first patient treated
developed a sterile buttock abscess [3]. Although Banting, Best, Collip and Macleod
subsequently prepared more purified insulin extracts using acid-alcohol to dissolve the
insulin and prevent degradation by exocrine enzymes, Banting’s acceptance speech for the
1923 Nobel Prize in Physiology and Medicine concluded with these words:
“Insulin is not a cure for diabetes; it is a treatment. It enables the diabetic to burn
sufficient carbohydrates, so that proteins and fats may be added to the diet in sufficient
quantities to provide energy for the economic burdens of life [3].”
Cells 2021, 10, 278. https://doi.org/10.3390/cells10020278 https://www.mdpi.com/journal/cells