A More Persistent Tolerance to Islet Allografts Through Bone Marrow Transplantation in Minimal Nonmyleoablative Conditioning Therapy B.-W. Lee, J.I. Lee, S.H. Oh, Y.R. Ahn, H.Y. Chae, M.S. Lee, M.K. Lee, and K.W. Kim ABSTRACT Introduction. Islet transplantation is a therapeutic approach to prevent diabetes compli- cations. However, the side effects of the required lifelong immunosuppressive regimens to prevent graft rejection restrict the impact of type 1 diabetes. One strategy to overcome these limitations is tolerance induction and graft acceptance through hematopoietic chimerism. In this study we investigated whether tolerance to major histocompability complex (MHC) and minor-disparate islet allografts could be induced by minimal nonmyeloablative conditioning and whether more persistent donor-specific islet allografts were accepted if the grafts were implanted with simultaneous bone marrow cells. Methods. The donor and recipient mice were BALB/c(H-2 b ) and C57BL/6(H-2 d ), respectively. In group 1 streptozotocin-induced diabetic C57BL/6(H-2 d ) mice received only 500 islets of BALB/c(H-2 b ). Group 2 recipients conditioned with antilymphocyte serum, 100 cGy total body irradiation and cyclophosphamide were given islet cells of BALB/c(H-2 b ), but group 3 were simultaneously given 30 10 6 BALB/c(H-2 b ) mice BMCs and islet cells similar to group 2. Results. We obtained 5% to 6% allogeneic donor chimerism and 60% graft survival at 80 days after islet transplantation in group 3. We observed lymphocyte infiltration around the islet without destruction of endocrine cells and the presence of strong insulin/glucagon- stained cells in group 3. Conclusion. This minimal nonmyeloablative conditioning therapy induced donor chi- merism and immune tolerance between MHC- and minor-disparate (BALB/c¡C57BL/6) mice and long-term islet graft survival was obtained through cotransplantation of bone marrow cells. I SLET TRANSPLANTATION (IT) is a therapeutic op- tion to prevent diabetes complications for insulin- deficient patients state. However, the side effects of lifelong immunosuppressive regimens to prevent graft rejection restrict this treatment for type I diabetes. One strategy to overcome these limitations is tolerance induction and graft acceptance through hematopoietic chimerism. 1 Although several tolerance approaches 1–4 have been tried, the role of bone marrow cells (BMCs) in conditioning experiments has not been fully elucidated. In this study, we investigated whether tolerance to major histocompability complex (MHC)- and minor-disparate islet allografts was induced by a minimal nonmyeloablative conditioning regimen and whether more persistent acceptance of donor-specific islet allografts was obtained if they were implanted with simul- taneous BMC transplantation. MATERIALS AND METHODS Animals Donor and recipient mice purchased from the CriBgi of Cheles River Technology were 12- to 13-week old inbred male BALB/c (H-2 b ) and 10- to 11-week-old inbred male C57BL/6(H-2 d ), respec- tively. From the Division of Endocrinology and Metabolism (B.-W. L., S.-H. O., M.-S. L., M.-K. L., K.-W. K.), Department of Medicine, Samsung Medical Center, Sungkyunkwan University School of Medicine and Samsung Biomedical Research Institute (J.-I. L., Y.-R. A., H.-Y. C.), Seoul, Korea. Address reprint requests to Kwang-Won Kim, Division of Endocrinology and Metabolism, Department of Medicine, Sam- sung Medical Center, Sungkyunkwan University School of Med- icine, 50 Ilwon-dong, Kangnam-ku, Seoul 135-710, Korea. E-mail: kwwkim@smc.samsung.co.kr 0041-1345/05/$–see front matter © 2005 by Elsevier Inc. All rights reserved. doi:10.1016/j.transproceed.2005.03.044 360 Park Avenue South, New York, NY 10010-1710 2266 Transplantation Proceedings, 37, 2266 –2269 (2005)