718 Medicinal Chemistry, 2011, 7, 718-726 1573-4064/11 $58.00+.00 © 2011 Bentham Science Publishers Cloning, Expression and Characterization of Mouse (Mus musculus) Nicotinamide 5'-Mononucleotide Adenylyltransferase-2 David W. Raches 1 , Suhong Xiao 2 , Praveen Kusumanchi 3 , Joel Yalowitz 2 , Paresh Sanghani 1 , Eric C. Long 4 , Aok C. Antony 2,3 and Hiremagalur N. Jayaram 1,3, * 1 Department of Biochemistry and Molecular Biology, and 2 Department of Medicine, Indiana University School of Medi- cine, Indianapolis, USA; 3 Richard L. Roudebush Veterans Affairs Medical Center, Indianapolis, USA; 4 Department of Chemistry and Chemical Biology, Indiana University-Purdue University Indianapolis (IUPUI), Indianapolis, USA Abstract: Nicotinamide adenine dinucleotide (NAD + ) is synthesized by the action of nicotinamide mononucleotide adenylyltransferase (NMNAT) from NMN and ATP. The mouse homolog of NMNAT-2 (mmNMNAT-2) was cloned, expressed, and subsequently identified using MALDI-TOF in conjunction with the ProFound database. Circular dichroism analyses of recombinant mmNMNAT-2 showed helical and sheet secondary structures, consistent with the known structure of the human isoform. Competition experiments using mouse pancreatic tissue lysates with recombinant mmNMNAT-2 demonstrated that the activity of the expressed protein was similar to the human isoform. Immunohisto- chemistry of mouse embryonic tissues with hNMNAT-2 also showed a tissue- and cellular-specific expression of this iso- form. Therefore, our studies demonstrate for the first time the clear biological evidence for the existence of a mouse iso- form of hNMNAT-2. These studies may help in future investigations aimed at understanding the regulation of this gene and its pathway, and in turn, will spur the development of novel therapies for diseases such as cancer and diabetes since mice are the most frequently used experimental system for in vivo studies. Keywords: Circular dichroism, MALDI-TOF, mouse NMNAT-2, tissue expression, NAD, tiazofurin. INTRODUCTION Many of the enzymatic reactions that mediate cellular processes require high-energy electron carrier nucleotides such as nicotinamide adenine dinucleotide (NAD + ). Thus, the biosynthetic pathways leading to these essential carriers provide potential loci for anti-cancer drug development and interdiction. NAD + required for cellular viability is synthe- sized by the enzymatic action of nicotinamide mononucleo- tide adenylyltransferase (NMNAT) from nicotinamide mononucleotide (NMN) and adenosine triphosphate (ATP) [1]. Biosynthesis of NAD + occurs either by: (1) a double displacement reaction leading to pyrophosphate (PP i ) release and transfer of an adenylyl group to NMN; or by (2) a nu- cleophilic attack of the 5'-phosphate of the NMN on the - phosphate of ATP releasing pyrophosphate and the product dinucleotide (Fig. 1a). Two conserved pathways for NAD + synthesis i.e., de novo and salvage pathways, respectively, depend upon NMNAT to catalyze the final, rate-limiting reaction of NMN or nicotinic acid mononucleotide with ATP to form NAD + or nicotinic acid adenine dinucleotide and PP i (Fig. 1b) underscoring the fundamental importance of this enzyme [2]. The reactive portion of NAD + is the nicotinamide ring, a pyridine derivative synthesized from vitamin B6 (niacin). NAD + is utilized as a substrate for many enzymes such as *Address correspondence to this author at the Richard L. Roudebush Veter- ans Affairs Medical Center-151, 1481 West Tenth street, Indianapolis, Indi- ana, 46202, USA; Tel: 317-988-2479; Fax: 317-988-3180; E-mail: hjayaram@iupui.edu O N O OH HO P O O - - O O NH 2 O N O OH HO P O O - O + P O O - O P O - - O O NMN ATP N N N NH 2 O O OH HO P O O - O P O O - O N O NH 2 + O N HO HO N N N NH 2 NAD + PP i O - P O O - O P O - - O O + Fig. (1a). Schematic illustration of NMNAT’s enzymatic reaction to form NAD + and PP i from NMN and ATP. L-Tryptophan Quinolinic acid Nicotinic acid mononucleotide Nicotinic acid adenine dinucleotide (NaAD) Nicotinic acid (Na) Nicotinamide (Nam) Nicotinamide mononucleotide (NMN) Nicotinamide riboside (NR) NRK NaPRTase NamPRTase NMNAT NAD + NAD Synthase QAPRTase NMNAT de novo Pathway Salvage Pathways Fig. (1b). Illustration of the biosynthetic pathways for NAD synthesis. QAPRTase: quinolinic acid phosphoribosyltransferases; NAD synthase: nicotinamide adenine dinucleotide synthase; NaPR- Tase: nicotinic acid phosphoribosyltransferase; NamPRTase: nicotinamide phosphoribosyltransferase; NRK: nicotinamide ribose kinase.