chemosensors
Article
Expediting Disulfiram Assays through a Systematic Analytical
Quality by Design Approach
João Basso
1,2
, Maria Luísa Ramos
2
, Alberto Pais
2
, Rui Vitorino
3,4,5
, Ana Fortuna
1,6
and
Carla Vitorino
1,2,
*
Citation: Basso, J.; Ramos, M.L.; Pais,
A.; Vitorino, R.; Fortuna, A.; Vitorino,
C. Expediting Disulfiram Assays
through a Systematic Analytical
Quality by Design Approach.
Chemosensors 2021, 9, 172.
https://doi.org/10.3390/
chemosensors9070172
Academic Editor: Cláudia Maria
Rosa Ribeiro
Received: 30 April 2021
Accepted: 3 July 2021
Published: 6 July 2021
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1
Faculty of Pharmacy, University of Coimbra, 3000-548 Coimbra, Portugal; joaobasso@ff.uc.pt (J.B.);
afortuna@ff.uc.pt (A.F.)
2
Coimbra Chemistry Centre, Department of Chemistry, University of Coimbra, 3004-504 Coimbra, Portugal;
mlramos@ci.uc.pt (M.L.R.); pais@qui.uc.pt (A.P.)
3
iBiMED—Department of Medical Sciences, University of Aveiro, 3810-193 Aveiro, Portugal; rvitorino@ua.pt
4
UnIC—Cardiovascular Research & Development Centre, Department of Surgery and Physiology,
Faculty of Medicine, University of Porto, 4200-319 Porto, Portugal
5
QOPNA & LAQV-REQUIMTE, Chemistry Department, University of Aveiro, 3810-193 Aveiro, Portugal
6
Coimbra Institute for Biomedical Imaging and Translational Research, University of Coimbra,
3000-548 Coimbra, Portugal
* Correspondence: csvitorino@ff.uc.pt
Abstract: An Analytical Quality by Design (AQbD) approach is presented, aiming at the development
and validation of an HPLC method for the quantification of disulfiram and copper diethyldithio-
carbamate in lipid nanoparticles. Following the definition of the analytical target profile (ATP),
encompassing the critical analytical attributes (CAA), a two-level risk assessment strategy (Ishikawa
diagram—failure mode and effect analysis (FMEA)) was employed to identify the critical method
parameters (CMPs) with an extensive impact on method performance. The behavior of the CMPs
(flow rate and mobile phase composition) was further characterized by experimental design, resorting
to a face-centered central composite design (FcCCD). Statistical modeling, response surface analysis,
and Monte Carlo simulations led to the definition of the Method Operable Design Region (MODR),
associated with a negligible risk of failing the predefined CAA specifications. The optimal method
was validated according to international regulatory recommendations. Apart from guaranteeing
linearity, accuracy, precision, specificity, robustness, and stability, these conditions were found to be
suitable for analysis using a different HPLC column and equipment. In a nutshell, the development
and optimization strategies, under the comprehensive framework of AQbD, provided an effective,
simple, rapid, reliable, and flexible method for routine analysis of the compounds in research or
industrial environments.
Keywords: AQbD; cancer; central composite design; copper diethyldithiocarbamate; disulfiram;
lipid nanoparticles; liquid chromatography; method optimization; method robustness; MODR
1. Introduction
Disulfiram (DSF) is a dithiocarbamate derivative with clinical application to treat
alcohol addiction. It blocks ethanol metabolism by inhibiting hepatic aldehyde dehydroge-
nases 1 and 2, thus increasing acetaldehyde blood levels. Consequently, alcohol consumers
experience nausea, sweating, hypotension, respiratory difficulties, and other alcoholic
intoxication symptoms, thereby rejecting additional beverages [1]. In parallel, DSF shows
promising in vitro/in vivo results against several types of neoplastic diseases, as it may act
over 19 different targets/pathways to reduce cancer cell viability [2]. DSF is also a chelating
compound, producing copper (II) diethyldithiocarbamate (Cu(DDC)
2
) in the presence of
endogenous or exogenous copper (II) ions. Alternatively, Cu(DDC)
2
can be synthesized by
chelating copper with sodium diethyldithiocarbamate (Figure 1)[3,4]. Interestingly, this
Chemosensors 2021, 9, 172. https://doi.org/10.3390/chemosensors9070172 https://www.mdpi.com/journal/chemosensors