Pediatric and Developmental Pathology 17, 406-408, 2014
DOI: 10.2350/14-06-1501-CR.1
© 2014 Society for Pediatric Pathology
Pediatric Gastrointestinal PEComas:
A Diagnostic Challenge
M arco Pizzi , 1* I da di Lor enzo ,2 Emanuele S. d 'A mo r e ,3 Paolo D 'A ngelo ,4 and Rit a A laggio 1
department of Medicine-DIMED, General Pathology & Cytopathology Unit, University of Padova, Padova, Italy
2Pathology Unit, ARNAS Civico, Di Cristina and Benfratelli Hospital, Palermo, Italy
3Pathology Department, "San Bortolo” Hospital, Vicenza, Italy
4Pediatric Hematology and Oncology Unit, ARNAS Civico, Di Cristina and Benfratelli Hospital, Palermo, Italy
Received June 1, 2014; accepted July 14, 2014; published online July 14, 2014.
ABSTRACT
Perivascular epithelioid cell tumors (PEComas) in the
pediatric population are very rare and frequently arise in
the gastrointestinal tract. These tumors are characterized
by variable morphological and immunohistochemical
features, which may pose significant problems in
differential diagnosis with other gastrointestinal mesen
chymal tumors in pediatric patients. In presenting an
unusual pediatric case of gastrointestinal PEComa, we
also discuss the possible differential diagnosis of this rare
entity.
Key words: clear cell sarcoma, gastrointestinal mesen
chymal tumors, PEComa, pediatric pathology, SOX 10
INTRODUCTION
Perivascular epithelioid cell tumors (PEComas) represent
a broad family of mesenchymal neoplasms, characterized
by peculiar morphological and immunohistochemical
features. According to the current World Health Organi
zation Classification of Tumors of Soft Tissues, the
PEComa family encompasses several entities, including
angiomyolipoma, pulmonary clear cell “ sugar” tumors,
lymphangioleiomyomatosis, and unusual clear cell neo
plasms of various anatomic origins [1],
A recent survey by Doyle et al. indicated that
gastrointestinal (GI) PEComas are characterized by
unique morphological and immunohistochemical fea
tures; this poses relevant problems in the differential
diagnosis with other mesenchymal neoplasms of the GI
tract [2], As such, GI PEComas can represent a diagnostic
challenge, that only ancillary techniques (ie, immunohis-
tochemistry and cytogenetics) can help to resolve.
In the present case, we report the clinicopathological
features of a pediatric case of primary intestinal PEComa
and discuss the possible differential diagnosis of this
extremely rare entity.
* Corresponding author, e-mail: marcopizzi2002@yahoo.it
CASE REPORT
An 8-year-old Caucasian girl presented at Di Cristina and
Benfratelli Hospital (Palermo, Italy) with mild abdominal
tenderness and epigastric pain. Computed tomographic
scan revealed an intraperitoneal mass (greater diameter
8 cm) that was partially adherent to the transverse colon.
After surgical excision (complete resection with negative
margins [RO]), gross examination revealed a roundish,
pedunculated lesion with focal hemorrhagic areas.
Histologic examination revealed that the tumor was
composed of a fascicular proliferation of spindle to
epithelioid cells, focally arranged in a storiform growth
pattern. Intratumor blood vessels were tiny and incon
spicuous, with fascicles of neoplastic cells often arranged
around them. Despite the presence of occasional hemor
rhagic areas, tumor coagulative necrosis was consistently
absent. The neoplastic population was composed of
medium-sized, spindle to polygonal elements, with
amphophilic cytoplasm, elongated nuclei, finely dispersed
chromatin, and an absence of evident nucleoli. The
mitotic rate was extremely low (<2 mitoses/10 HPF)
(Fig. 1A,B).
At immunohistochemistry, neoplastic cells were
positive for Melan-A, HMB-45, MiTF, c-Kit, and NSE,
with consistent negativity for TFE3, desmin, smooth
muscle actin (SMA), muscle-specific actin (MSA), SI00,
and SOX 10 (Table 1 and Fig. 1C-F). Fluorescent in situ
hybridization analysis did not demonstrate EWS gene
translocations or other recurrent chromosomal aberrations.
The overall clinical, morphological, immunohisto
chemical, and cytogenetic data led to a final diagnosis of
primary gastrointestinal PEComa. At present (8 months
after clinical presentation) the patient is alive with no
evidence of relapsing/recurring disease.
DISCUSSION
PEComas in the pediatric population are very rare and
frequently arise in the GI tract (10 of 37 cases reported in
the literature) [3-5]. Unlike their adult counterpart,