Cell Transplantation, Vol. 5, No. 2, pp. 327-337, 1996
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Original Contribution
CLINICAL STUDY OF FETAL MESENCEPHALIC INTRACEREBRAL TRANSPLANTS
FOR THE TREATMENT OF PARKINSON'S DISEASE
OLEG V. KOPYOV,*'
1
DEANE "SKIP" JACQUES,* ABRAHAM LIEBERMAN,! CHRISTOPHER M. DUMA,* AND
ROBERT L. ROGERS*
*Neurosciences Institute, Good Samaritan Hospital, Los Angeles, CA 90017 USA and tBarrow Neurological Institute, Phoenix, AZ USA
• Abstract — This study reports our findings from 22 pa-
tients (ages ranging from 42 to 73 yr; mean = 55.2) with
recalcitrant idiopathic Parkinson's disease (PD) who re-
ceived implants of fetal ventral mesencephalic tissue using
an MRI-guided stereotactic procedure and who have been
followed for at least 6 mo postoperatively, employing the
guidelines established by the Core Assessment Program for
Intracerebral Transplantations. Evaluations were video-
taped and were performed both on and off levodopa medi-
cations. To date, we have seven patients with 24 mo, three
with 18 mo, three with 12 mo, and nine with 6 mo of post-
surgical assessments. Comparing surgical outcomes to lev-
els prior to fetal transplants we found: 1) mean levodopa
levels were reduced 46% at 6 mo, 12% at 12 mo, 20% at 18
mo, and 54% at 24 mo; 2) Unified Parkinson's Disease
Rating Scale (UPDRS) scores with patients on levodopa
were improved by an average of 38% (6 mo), 50.2% (12
mo), 69.3% (18 mo), and 73.9% (24 mo), while off medica-
tion scores showed reductions ranging from 24.7% at 6 mo
to 55.1% at 24 mo. Other measures, including Hoehn-Yahr
staging, Activities of Daily Living, and dyskinesia rating
scales, were also significantly improved following fetal
transplants. Timed motor tasks (finger dexterity, supina-
tion-pronation, foot tapping, and Stand-Walk-Sit) perfor-
mance also demonstrated highly significant improvements.
Patient's self-rating scores indicated that the patients typi-
cally perceived substantial improvements in their condi-
tion. However, substantial variability in the improvements
following surgery still persists and range from nominal im-
provements in performance to significant changes that can
be classified as altering the overall lifestyle of the patients.
To date, 4 of the 22 subjects were considered by the phy-
sicians to be nonresponders; that is, there were no clinically
relevant improvements in these patients' conditions.
• Keywords — Fetal transplantation; Parkinson's disease.
INTRODUCTION
Recent evidence from both animal and preliminary hu-
man clinical studies has indicated that neural transplan-
tation of ventral mesencephalic fetal tissue offers prom-
ise of ameliorating the symptomatology of Parkinson's
disease (PD), especially among patients who are refrac-
tory to pharmacological treatment. A large number o f P D
patients who have been on levodopa therapy for ex-
tended periods of time eventually show reduced respon-
siveness to drug interventions and develop severe dis-
abling symptoms. PD has received a majority of the
attention of neurotransplantation programs because of
the strong relationship of this disease to the single neu-
rotransmitter dopamine (DA). Early histological studies
were able to demonstrate a loss of DA-producing cells in
the pars compacta of the substantia nigra among PD
patients (11). This finding, combined with substantial
evidence that pharmacological replacement of DA re-
sulted in substantially reduced somatic anomalies in both
human PD patients and animal models, (3,8,9), suggests
that intracerebral replacement of DA-secreting cells has
the potential to benefit these patients.
Clinical studies in humans of fetal tissue transplants
have been less consistent and have often reported short-
term results among small groups of subjects. Several
early reports between 1987 and 1991 indicated that some
level of recovery was measurable in most patients, but
therapeutic value regarding the degree of recovery was
questionable (13,15,17). However, three recent reports
published in the same issue of the New England Journal
ACCEPTED 10/13/95. Good Samaritan Hospital, 637 South Lucas Avenue, Suite
'Correspondence should be addressed to Oleg Kopyov, #501, Los Angeles, CA 90017-2395.
Ph.D., M.D., Neurotransplantation, Neurosciences Institute,
327