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C
URRENT
O
PINION
Mesenchymal stromal cells as a means of
controlling pathological T-cell responses in
allogeneic islet transplantation
James L. Reading
a
, Shereen Sabbah
a
, Sarah Busch
b
, and Timothy I.M. Tree
a
Purpose of review
To evaluate the potential for mesenchymal stromal cells (MSCs) to regulate T-cell responses responsible for
graft destruction following allogeneic islet transplantation (AIT).
Recent findings
Despite a high level of primary graft function being observed in most individuals following AIT, the majority
of recipients require exogenous insulin within 5 years, presumably due to graft attrition. Although this
process is not fully understood, recent evidence suggests that a combination of chronic allograft rejection
and/or the recrudescence of anti-islet autoimmunity govern islet loss. Emerging reports highlight that the
pathology of AIT may involve the proliferation, effector function and homeostatic expansion of alloreactive
and autoreactive T-cell pools. MSCs exhibit several desirable characteristics, which may advocate their use
in AIT. This includes the capacity to suppress alloreactive and autoimmune T-cell responses, and promote a
cytokine environment that is likely to be graft protective. However, further work is needed to clarify if MSCs
can function in the setting of immune suppression and discern how they may effect T-cell effector functions
and influence homeostatic expansion.
Summary
MSCs exhibit the potential to regulate the T-cell-driven processes that underlie disease pathology in AIT, but
further study may be required to maximize their therapeutic efficacy.
Keywords
allogeneic islet transplantation, MSC, T cell, T1D
INTRODUCTION
Research over the past 35–40 years has demonstrated
that type 1 diabetes mellitus (T1D) is a T-cell-medi-
ated autoimmune disease in which the destruction of
insulin secreting b-cells is driven by islet-specific T
cells; leading to loss of insulin production and
glycemic control [1]. The administration of exogen-
ous insulin is unable to completely mimic physio-
logic insulin secretion and, combined with the failure
of glucose counter-regulation, increases the risk of
severe hypoglycemia, and secondary vascular com-
plications.
Allogeneic islet transplantation (AIT) can pro-
vide long-term improvements in glycemic control,
enhancing the overall quality of life in the majority
of recipients. However, the shortage of donor
organs, high cost of islet isolation and the require-
ment for life-long immunosuppression means this
procedure is currently reserved for a select group
of T1D patients with negative fasting C-peptide
(<0.3 ng/ml), severe glycemic lability, hypoglyce-
mia unawareness and consistently elevated HbA
1c
levels (>8%) [2,3].
The success rate of islet transplantation was
improved significantly by the introduction of the
Edmonton protocol in 2000. This landmark trial
demonstrated the successful reversal of T1D in all
seven patients using a glucocorticoid-free immuno-
suppressive regimen at 1 year [4]. However, the
5-year follow-up of this cohort revealed eventual
loss of b-cell function and recurrence of diabetes,
a
Department of Immunobiology, King’s College London, Guy’s Hospital,
London, UK and
b
Athersys, Inc., Cleveland, Ohio, USA
Correspondence to Dr Timothy Tree, Department of Immunobiology,
King’s College London, 3rd Floor, Borough Wing, Guy’s Hospital,
London SE1 9RT, UK. Tel: +44 207 188 1182; e-mail: Timothy.Tree
@kcl.ac.uk
Curr Opin Organ Transplant 2013, 18:59–64
DOI:10.1097/MOT.0b013e32835c2adf
1087-2418 ß 2013 Wolters Kluwer Health | Lippincott Williams & Wilkins www.co-transplantation.com
REVIEW