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ISSN: 2168-9296
Cell & Developmental Biology
Alam, Cell Dev Biol 2016, 5:2
http://dx.doi.org/10.4172/2168-9296.1000172
Volume 5 • Issue 2 • 1000172
Cell Dev Biol
ISSN: 2168-9296 CDB, an open access journal
Open Access Review Article
Methylenetetrahydrofolate Reductase Gene Polymorphisms and
Cardiovascular Diseases
Mohammad Afaque Alam*, Ph.D
Department of Pediatrics, College of Medicine, Drexel University, Philadelphia, PA, USA
Abstract
A growing body of evidence suggests that mutations in MTHFR gene are involved in cardiovascular diseases
(CVD) - cardiac development, atherosclerosis, myocardial infarction, heart failure, hypertension, aneurysms- and
several other disease- cancers, neurological and metabolic disorders. Genetic variations in other genes are added
risk for CVD- a leading cause of morbidity and mortality around the globe. Accumulating data over the decade has
enhanced our understanding of MTHFR defciency and diseases associated risk. The frequency of MTHFR 677 C→T
and 1298 A→C gene mutations varies substantially in different regions of the world among different racial and ethnic
groups. In particular, 677C→T and 1298 A→C variant are associated with clinical manifestation of almost all non-
communicable diseases. This review describes the roles of MTHFR gene mutation in CVD and prospective therapies
for heart disease treatment.
*Corresponding author: Mohammad Afaque Alam, Department of Pediatrics,
College of Medicine, Drexel University, 894 Union Ave, Memphis,, TN 38103, USA,
Tel: +1-901-518-6443; E-mail: aafaqq@gmail.com
Received May 09, 2016; Accepted May 13, 2016; Published May 21, 2016
Citation: Alam MA (2016) Methylenetetrahydrofolate Reductase Gene
Polymorphisms and Cardiovascular Diseases. Cell Dev Biol 5: 172.
doi:10.4172/2168-9296.1000172
Copyright: © 2016 Alam MA. This is an open-access article distributed under the
terms of the Creative Commons Attribution License, which permits unrestricted
use, distribution, and reproduction in any medium, provided the original author and
source are credited.
Keywords: Polymorphism; MTHFR gene; Mutations; Cardiac diseases
Methylenetetrahydrofolate Reductase (MTHFR) Gene
Methylenetetrahydrofolate reductase (MTHFR) is a cytosolic
enzyme, which contains a non-covalently bound Flavin Adenine
Dinucleotide (FAD) cofactor and uses NADPH as the reducing
agent. Tis is an essential enzyme for folate and homocysteine (hcy)
metabolisms and exhibits a risk factor for a number of heart diseases
[1,2]. MTHFR is responsible for converting the circulating form of
folate 5,10-methylenetetrahydrofolate to 5-methyltetrahydrofolate
in multistep processes that converts homocysteine- an amino acid
to another amino acid, methionine and S-adenosyl methionine - the
common methyl donor for the maintenance of several biological
processes (Figure 1). Te body uses methionine to make proteins and
other important compounds for growth and metabolism. On the other
hand, appropriate methylation facilitates the clearance of harmful
substances, metabolites and waste products more efciently.
Over the decade researchers have enhanced our understanding of
pathophysiological relation with common and rare MTHFR mutations,
enzyme defciency, elevated hcy and low folate levels in circulation. Of
note, it has been reported that compromised MTHFR enzyme activity
leads to elevated levels of hcy. Homocysteine is a sulpher containing
amino acid, is an oxidant, and play a vital role in oxidation of lipids and
lipoproteins, hence augmenting CVD risk [3,4]. Mudd et al. [5] have
discovered a severe form of MTHFR enzyme defciency, which leads to a
very serious health conditions- homocysteinuria - in which hcy excretes
out in urine. Since the discovery of the role of MTHFR gene mutation in
human diseases, this enzyme has received much interest in establishing
the association with increased concentration of hcy and heart diseases.
Tere are several case control, retrospective and meta analyses that have
demonstrated that MTHFR polymorphism is associated with increased
blood hcy concentration and CVD [3,6-9]. Te MTHFR 677C→T and
1298 A→C homozygous genotype is associated with premature CAD
and other cardiovascular disorders [1,2,10].
On the other hand in the mid-nineties a great piece of discovery
- cDNA synthesis - has been published, which paved the way for
functional analysis of the MTHFR gene [11]. Tis transformed the
MTFHR research which followed by identifcation of several rare and
common variants including missense variant of alanine to valine at
nucleotide 677, which encodes the thermolabile form of the enzyme
[3,12].
Te mutant TT genotype is linked to elevated circulating hcy
levels and the individuals carrying this mutation exhibits low folate
levels [13]. 677C→T variant is the most common and prevalent form
of MTHFR genetic polymorphisms, which depicts mild to high level
of hcy and associated disease manifestation [13-15]. Nonetheless, this
variant located in the catalytic domain of the gene and thermolabile
in nature afects hcy and folate metabolism. In 1998, another common
polymorphism in the MTHFR gene was described, the 1298 A→C
transition, which caused an amino acid substitution of glutamate
by alanine [16,17]. Sibani et al. [18] reported 33 severe mutation
and two common mutations, however Martin et al. [19] reported 65
mutations in MTHFR gene. MTHFR- as a central modulator of folate-
hcy-methionine pathway, inspired investigators from all felds to
identify and characterize novel mutations in relation to human health.
Terefore hundreds (~ 109) of polymorphism - that includes mutations,
deletions, duplications, and splicing variants- have been identifed [19]
and investigations continue to establish the role in CVD risk [20].
Correspondingly, to explore the cause of diseases pathology as a
consequence of MHFR gene mutation, scientists developed Mthfr
knockout mice. Tey have exhibited a remarkably lower (>60%) enzyme
activity in 677C→T variant, resulting in high hcy level among mutant
group and also observed high lipid deposition in the major arteries [21].
Cascading efect of hyperhomocysteinemia is the causative factor for
high cholesterol deposition in the vessel which initiates atherosclerosis
generation and progression, that would lead to myocardial infarction
and heart failure. MTHFR gene exists in dimeric form, consisting of
656 amino acid translating a protein that migrates at ~ 74-77 kDa. Tis
is an evolutionary conserved gene throughout organisms from yeast
to human. However, mouse depicts the highest homology (>90%).
MTHFR gene is located at the short arm of chromosome 1 (1p36.3) and