Accepted Article Preview: Published ahead of advance online publication
Deletion of the GAA repeats from the human frataxin gene
using the CRISPR-Cas9 system in YG8R-derived cells and
mouse models of Friedreich Ataxia
D L Ouellet, K Cherif, J Rousseau, J-P Tremblay
Cite this article as: D L Ouellet, K Cherif, J Rousseau, J-P Tremblay, Deletion of
the GAA repeats from the human frataxin gene using the CRISPR-Cas9 system in
YG8R-derived cells and mouse models of Friedreich Ataxia, Gene Therapy
accepted article preview 26 December 2016; doi: 10.1038/gt.2016.89.
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Received 8 November 2016; accepted 19 December 2016; Accepted article
preview online 26 December 2016
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