Clinical Otolaryngology. 2020;45:695–702. wileyonlinelibrary.com/journal/coa | 695 © 2020 John Wiley & Sons Ltd
Received: 28 October 2019
|
Revised: 23 April 2020
|
Accepted: 27 April 2020
DOI: 10.1111/coa.13560
ORIGINAL ARTICLE
Treacher Collins syndrome: A novel TCOF1 mutation and
monopodial stapes
Piranit Nik Kantaputra
1,2,3
| Kanich Tripuwabhrut
4
| Worrachet Intachai
1
|
Bruce M. Carlson
5
| Natalina Quarto
6
| Chumpol Ngamphiw
7
| Sissades Tongsima
7
|
Nuntigar Sonsuwan
8
1
Center of Excellence in Medical Genetics
Research, Chiang Mai University, Chiang
Mai, Thailand
2
Division of Pediatric Dentistry, Department
of Orthodontics and Pediatric Dentistry,
Faculty of Dentistry, Chiang Mai University,
Chiang Mai, Thailand
3
Dentaland Clinic, Chiang Mai, Thailand
4
Division of Orthodontics, Department
of Orthodontics and Pediatric Dentistry,
Faculty of Dentistry, Chiang Mai University,
Chiang Mai, Thailand
5
Department of Anatomy and Cell Biology,
University of Michigan, Ann Arbor, MI, USA
6
Department of Surgery, Division of Plastic
and Reconstructive Surgery, Stanford
University School of Medicine, Stanford,
CA, USA
7
National Biobank of Thailand, National
Center for Genetic Engineering and
Biotechnology (BIOTEC), Thailand Science
Park, Pathum Thani, Thailand
8
Department of Otolaryngology, Faculty
of Medicine, Chiang Mai University, Chiang
Mai, Thailand
Correspondence
Piranit Nik Kantaputra, Division of Pediatric
Dentistry, Department of Orthodontics and
Pediatric Dentistry, Faculty of Dentistry,
Chiang Mai University, Chiang Mai 50200,
Thailand.
Email: dentaland17@gmail.com
Funding information
Faculty of Dentistry, Chiang Mai University,
Grant/Award Number: NA; Dental
Association of Thailand, Grant/Award
Number: NA; Thailand Research Fund,
Grant/Award Number: NA
Abstract
Treacher Collins syndrome (TCS: OMIM 154500) is an autosomal dominant craniofa-
cial disorder belonging to the heterogeneous group of mandibulofacial dysostoses.
Objective: To investigate four Treacher Collins syndrome patients of the Sgaw Karen
family living in Thailand.
Method: Clinical examination, hearing tests, lateral cephalometric analyses,
Computed tomography, whole exome sequencing and Sanger direct sequencing
were performed.
Results: All of the patients affected with Treacher Collins syndrome carried a novel
TCOF1 mutation (c.4138_4142del; p.Lys1380GlufsTer12), but clinically they did not
have the typical facial gestalt of Treacher Collins syndrome, which includes down-
ward-slanting palpebral fissures, colobomas of the lower eyelids, absence of eye-
lashes medial to the colobomas, malformed pinnae, hypoplastic zygomatic bones and
mandibular hypoplasia. Lateral cephalometric analyses identified short anterior and
posterior cranial bases, and hypoplastic maxilla and mandible. Computed tomogra-
phy showed fusion of malleus and incus, sclerotic mastoid, hypoplastic middle ear
space with a soft tissue remnant, dehiscence of facial nerve and monopodial stapes.
Conclusion: Treacher Collins syndrome in Sgaw Karen patients has not been previ-
ously documented. This is the first report of monopodial stapes in a TCS patient who
had a TCOF1 mutation. The absence of a common facial phenotype and/or the pres-
ence of monopodial stapes may be the effects of this novel TCOF1 mutation.