Fax +41 61 306 12 34 E-Mail karger@karger.ch www.karger.com Original Research Article Dement Geriatr Cogn Disord 2006;22:48–53 DOI: 10.1159/000093261 Stability of CSF -Amyloid 1–42 and Tau Levels by APOE Genotype in Alzheimer Patients Edward D. Huey a Nadeem Mirza a Karen T. Putnam a Holly Soares c Gyorgy Csako b James A. Levy a Brittany Copenhaver a Robert M. Cohen a Trey Sunderland a a Geriatric Psychiatry Branch, b Department of Laboratory Medicine, W.G. Magnuson Clinical Center, National Institute of Mental Health, Bethesda, Md., and c Pharmacogenomics and Clinical Biochemical Measurements Division, Pfizer Central Research, Groton, Conn., USA Introduction Alzheimer’s disease (AD) is associated with neurof- brillary tangles composed of microtubule-associated pro- tein tau and the formation of plaques consisting primar- ily of -amyloid peptides. As new medications for AD are developed (e.g., secretase inhibitors, amyloid immuniza- tion), the correct early diagnosis of AD will become cru- cial, and CSF biomarkers will likely be a useful aid for early diagnosis. Prior to their clinical use, however, bio- markers should be shown to be informative over the course of the illness. High concentrations of tau and ab- normally low concentrations of -amyloid 1–42 in the ce- rebrospinal fuid (CSF) show promise as diagnostic tests for AD [1, 2], but their stability over time in AD and the efect of the APOE 4 allele, known to increase suscepti- bility to AD, on these measurements are not clear [3–8]. Tis experiment tests the stability over time, and the efect of APOE genotype, on CSF tau and -amyloid 1–42 . Te period of time previous authors have assessed the stability of CSF biomarkers has generally been 1–2 years [3–7], with one study measuring CSF -amyloid and tau for a mean period of 3 years [8] . Similarly, our laboratory found stability of CSF tau protein in mild-to-moderate AD patients over 2 years despite signifcant clinical pro- Key Words Alzheimer disease diagnostic tests Cerebrospinal fluid biomarker -Amyloid Tau APOE genotype Abstract Background: Cerebrospinal fluid (CSF) measures of -amy- loid 1–42 and tau differ between patients with Alzheimer’s Dis- ease (AD) and elderly normal controls. The effect of time and APOE genotype on these biomarkers continues to be eluci- dated. Methods: We assessed CSF -amyloid 1–42 and tau in 20 mild-to-moderate AD patients, 11 APOE 4+ and 9 APOE 4–, over a mean time of 3.8 years (range 1–11.1 years). Re- sults: Over the period measured, CSF -amyloid 1–42 levels were lower in APOE 4+ compared to APOE 4– patients, and the levels decreased over time. Tau levels were stable over time and did not show an effect of APOE allele. Conclusions: While this is a limited clinical sample, the further decrease in CSF -amyloid 1–42 (i.e., more abnormal) combined with the CSF tau stability over a mean period of almost 4 years sug- gests that -amyloid 1–42 and tau maintain their potential usefulness as diagnostic biomarkers over time. These find- ings should be taken into account if CSF -amyloid 1–42 and tau are used as measures of treatment response. Copyright © 2006 S. Karger AG, Basel Accepted: December 18, 2005 Published online: May 8, 2006 Edward D. Huey, MD Fellow, Cognitive Neuroscience Section National Institute of Neurological Disorders and Stroke Bldg. 10, Room 5C205, MSC 1440, Bethesda, MD 20892 (USA) Tel. +1 301 402 2584, Fax +1 301 480 2909, E-Mail hueye@ninds.nih.gov © 2006 S. Karger AG, Basel 1420–8008/06/0221–0048$23.50/0 Accessible online at: www.karger.com/dem