www.thelancet.com/oncology Vol 21 June 2020 843
Articles
Lancet Oncol 2020; 21: 843–50
See Comment page 745
Department of Experimental
Therapeutics (J Sato MD,
N Yamamoto MD), Clinical
Research Support Office
(K Nakamura MD, Y Nagasaka BS,
M Kawasaki MS, T Yamada MPH),
Department of Thoracic
Oncology (Y Ohe MD), and
Biostatistics Division, Center
for Research Administration
and Support (R Machida ME,
A Kuchiba PhD), National
Cancer Center Hospital, Tokyo,
Japan; Department of Thoracic
Oncology, Hyogo Cancer
Center, Hyogo, Japan
(M Satouchi MD, S Itoh MD);
Department of Thoracic
Oncology and Respiratory
Medicine, Tokyo Metropolitan
Cancer and Infectious Diseases
Center, Komagome Hospital,
Tokyo, Japan (Y Okuma MD);
Department of Thoracic
Oncology, National Cancer
Center Hospital East, Chiba,
Japan (S Niho MD); First
Department of Medicine,
Hokkaido University Hospital,
Hokkaido, Japan
(H Mizugaki MD); Division of
Thoracic Oncology, Shizuoka
Cancer Center, Shizuoka, Japan
(H Murakami MD); Department
of Respiratory Medicine and
Thoracic Oncology/Clinical
Research Center, Osaka Medical
College Hospital, Osaka, Japan
(Y Fujisaka MD); and
Department of Thoracic
Oncology and Medicine,
National Hospital Organization
Shikoku Cancer Center, Ehime,
Japan (T Kozuki MD)
Correspondence to:
Dr Noboru Yamamoto,
Department of Experimental
Therapeutics, National Cancer
Center Hospital,
Tokyo 104–0045, Japan
nbryamam@ncc.go.jp
Lenvatinib in patients with advanced or metastatic thymic
carcinoma (REMORA): a multicentre, phase 2 trial
Jun Sato, Miyako Satouchi, Shoichi Itoh, Yusuke Okuma, Seiji Niho, Hidenori Mizugaki, Haruyasu Murakami, Yasuhito Fujisaka, Toshiyuki Kozuki,
Kenichi Nakamura, Yukari Nagasaka, Mamiko Kawasaki, Tomoaki Yamada, Ryunosuke Machida, Aya Kuchiba, Yuichiro Ohe, Noboru Yamamoto
Summary
Background Thymic carcinoma is a rare malignant disease and standard treatment for advanced or metastatic thymic
carcinoma previously treated with platinum-based chemotherapy has not been established. Lenvatinib is a novel
multi-targeted inhibitor of VEGFR, FGFR, RET, c-Kit, and other kinases. The aim of this trial was to assess the activity
and safety of lenvatinib as a second-line treatment in thymic carcinoma.
Methods This single-arm, phase 2 trial done in eight institutions in Japan (fve cancer centres, two medical university
hospitals, and one public hospital) enrolled patients with pathologically confrmed unresectable advanced or
metastatic thymic carcinoma that progressed following at least one platinum-based chemotherapy. Key inclusion
criteria were age 20 years or older, at least one measurable lesion as defned by the Response Evaluation Criteria in
Solid Tumors version 1.1, and an Eastern Cooperative Oncology Group performance status of 0 or 1. Patients received
24 mg of lenvatinib orally once daily in 4-week cycles until disease progression or occurrence of unacceptable adverse
events. The primary endpoint was objective response rate evaluated at the data cutof date (Feb 22, 2019), by
independent central review in the intention-to-treat population. This trial is registered on JMACCT, JMA-IIA00285,
and on UMIN-CTR, UMIN000026777.
Findings Between April 21, 2017, and Feb 22, 2018, 42 patients were enrolled and all patients were included in the
activity and safety analysis. The median follow-up period was 15·5 months (IQR 13·1–17·5). The objective response
rate was 38% (90% CI 25·6–52·0, p<0·0001). 16 (38%) of 42 patients had a partial response and 24 (57%) had stable
disease. The most frequent grade 3 treatment-related adverse events were hypertension (27 [64%]) and palmar-plantar
erythrodysaesthesia syndrome (three [7%]). No patient died from adverse events.
Interpretation The activity and safety of lenvatinib in patients with advanced or metastatic thymic carcinoma was
confrmed. These results suggest that lenvatinib could become a standard treatment option for patients with
previously treated advanced or metastatic thymic carcinoma.
Funding Center for Clinical Trials, Japan Medical Association.
Copyright © 2020 Elsevier Ltd. All rights reserved.
Introduction
Thymic carcinoma is a rare malignant disease with an
incidence of about 0·02 per 100 000 person-years,
1,2
and
about 30% of patients have advanced disease at the time
of diagnosis. Patients with advanced or thymic carcinoma
have poor prognosis, and cytotoxic chemotherapies have
been used to achieve prolonged disease control in such
cases.
3
Several retrospective studies and phase 2 trials
have been done to investigate the efcacy of cytotoxic
agents, immune checkpoint inhibitors, and molecular
targeted drugs.
4–8
On the basis of the results of these
studies, platinum-based chemotherapy has been
recommended as a frst-line chemotherapy by some
practice guidelines.
9,10
However, standard second-line
treatment for advanced or metastatic thymic carcinoma
patients previously treated with platinum-based chemo-
therapy has not yet been established.
VEGF plays a key role in tumour angiogenesis, with a
negative efect on prognosis in various types of cancer.
VEGF receptors (VEGFR) are mainly classifed into
VEGFR1, VEGFR2, and VEGFR3. VEGFR2 expression
is an important mediator of VEGF-induced
angiogenesis, and VEGFR2 and PDGFR-α are known to
be activated in thymic carcinoma.
11–13
In our retrospective
analysis,
14
we analysed the antitumor activity of multi-
targeted kinase inhibitors in phase 1 trials. Several
phase 2 trials have reported the activity and safety of
multi-targeted kinase inhibitors, mainly targeting
VEGR, as second-line treatment for thymic carci-
noma.
5,8,11,15–17
The activity of sunitinib malate, a multi-
targeted kinase inhibitor targeting VEGFR, was tested
in 23 patients with thymic carcinoma and 16 patients
with thymoma in a phase 2 trial, in which six (26%) of
23 patients with thymic carcinoma achieved a partial
response.
5
Lenvatinib is a novel orally administered multi-targeted
kinase inhibitor for VEGFR, FGFR, c-Kit, and other
kinases, and has shown antitumour activity in several
cancer types.
18,19
Lenvatinib has been approved for the
treatment of thyroid cancer and hepatocellular cancer in